79. Homozygous familial hypercholesterolemia
128 clinical trials,   105 drugs   (DrugBank: 29 drugs),   8 drug target genes,   15 drug target pathways

Searched query = "Homozygous familial hypercholesterolemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

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1 trial found
No.TrialIDDate_
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Public_titleScientific_titleConditionInterventionPrimary_
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agemin
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agemax
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PhaseCountries
1NCT04080050
(ClinicalTrials.gov)
September 30, 20193/9/2019A Long-term Follow-up Study to Evaluate the Safety and Efficacy of RGX-501A Long-term Follow-up Study to Evaluate the Safety and Efficacy of RGX-501Homozygous Familial Hypercholesterolemia (HoFH)Drug: Single intravenous (IV) dose of human Low Density Lipoprotein Receptor (LDLR) Gene TherapyRegenxbio Inc.NULLEnrolling by invitation18 YearsN/AAll12United States;Canada;Italy;Netherlands