Rp-l401    (DrugBank: -)

1 disease
IDDisease name (Link within this page)Number of trials
326Osteopetrosis1

326. Osteopetrosis    [ 20 clinical trials,   52 drugs,   (DrugBank: 14 drugs),   16 drug target genes,   78 drug target pathways]
Searched query = "Osteopetrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 20 trial found
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1NCT04525352
(ClinicalTrials.gov)
October 202011/8/2020A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant OsteopetrosisA Phase I Clinical Trial for Gene Therapy in Infantile Malignant Osteopetrosis (IMO) to Evaluate the Safety and Preliminary Efficacy of Autologous CD34+ Enriched Cells Transduced With a LV Vector Encoding the TCIRG1 GeneInfantile Malignant OsteopetrosisBiological: RP-L401Rocket Pharmaceuticals Inc.NULLNot yet recruiting1 MonthN/AAll2Phase 1NULL