19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03201627 (ClinicalTrials.gov) | July 5, 2017 | 26/6/2017 | Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease | a Single-center, Prospective, Open, and Non-randomized Case-control Study of Lithium Carbonate Effect on Niemann Disease C1 Type | Niemann-Pick Disease, Type C1 | Drug: Lithium Carbonate | Xinhua Hospital, Shanghai Jiao Tong University School of Medicine | NULL | Active, not recruiting | 7 Years | 40 Years | All | 18 | Early Phase 1 | China |