19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT00316498 (ClinicalTrials.gov) | October 17, 2002 | 19/4/2006 | Saccadic Eye Movements in Patients With Niemann-Pick Type C Disease | A Phase I/II Randomized, Controlled Study of OGT 918 in Adult and Juvenile Patients With Niemann Pick C Disease | Niemann Pick Diseases | Drug: OGT918 | National Eye Institute (NEI) | NULL | Completed | 12 Years | N/A | All | 30 | Phase 1 | United States;United Kingdom |
| 2 | NCT00041535 (ClinicalTrials.gov) | July 5, 2002 | 9/7/2002 | OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease | A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease | Gaucher Disease | Drug: OGT 918 | National Institute of Neurological Disorders and Stroke (NINDS) | NULL | Completed | 4 Years | N/A | All | 30 | Phase 2 | United States;United Kingdom |