19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT01675674 (ClinicalTrials.gov) | September 2011 | 23/8/2012 | Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics | Unrecognized Mucopolysaccharidosis I, II, IVA, and VI in the Pediatric Rheumatology Population | Mucopolysaccharidoses;Mucopolysaccharidosis I;Mucopolysaccharidosis II;Mucopolysaccharidosis IV;Mucopolysaccharidosis VI | Other: Dried blood spot test for MPS | National MPS Society | MediResource Inc. | Terminated | 6 Months | 18 Years | Both | 3000 | N/A | United States |