257. 肝型糖原病 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 14 / 薬物数 : 27 - (DrugBank : 7) / 標的遺伝子数 : 3 - 標的パスウェイ数 : 8
薬物ごとの開発者(Primary Sponsor)、臨床試験情報(抜粋)です。
Antipyretic
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
Carbohydrates intake
University of British Columbia
2017 - NCT03218904 Canada;
Cornstarch
Hospital de Clinicas de Porto Alegre
2017 - NCT03871673 Brazil;
Dexamethasone (or equivalent)
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
EPHYNAL
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Empagliflozin
Children's Memorial Health Institute, Poland
2021 Phase 2 NCT04930627 Poland;
Cliniques universitaires Saint-Luc- Université Catholique de Louvain
2019 Phase 2 NCT04138251 Belgium;
Faxe Kondi Free
Rigshospitalet, Denmark
2015 - NCT02448667 Denmark;
Glucose intake
University of British Columbia
2017 - NCT03218904 Canada;
Glycosade
John Mitchell
2013 - NCT02054832 Canada;
University of Manitoba
2014 - NCT02176096 Canada;
H1 Blocker
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
H2 Blocker
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
MRNA che codifica l’enzima umano deramificante del glicogeno formulato in una nanopaticella lipidica
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
MRNA encoding the human glycogen debranching enzyme formulated in a lipid nanoparticle delivery
Ultragenyx Pharmaceutical Inc.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-ES Canada;France;Germany;Italy;Spain;United Kingdom;United States;
Ramipril
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Sweet polvilho
Hospital de Clinicas de Porto Alegre
2017 - NCT03871673 Brazil;
Tocopherol (vit E)
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Triheptanoin
Areeg El-Gharbawy
2020 Early Phase 1 NCT03665636 United States;
Baylor Research Institute
2009 Phase 2 NCT00947960 France;United States;
UX007
Copenhagen Neuromuscular Center
2018 Phase 2 EUCTR2017-004153-17-DK Denmark;
UX053
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
Ultragenyx Pharmaceutical Inc.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-ES Canada;France;Germany;Italy;Spain;United Kingdom;United States;
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
Carbohydrates intake
University of British Columbia
2017 - NCT03218904 Canada;
Cornstarch
Hospital de Clinicas de Porto Alegre
2017 - NCT03871673 Brazil;
Dexamethasone (or equivalent)
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
EPHYNAL
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Empagliflozin
Children's Memorial Health Institute, Poland
2021 Phase 2 NCT04930627 Poland;
Cliniques universitaires Saint-Luc- Université Catholique de Louvain
2019 Phase 2 NCT04138251 Belgium;
Faxe Kondi Free
Rigshospitalet, Denmark
2015 - NCT02448667 Denmark;
Glucose intake
University of British Columbia
2017 - NCT03218904 Canada;
Glycosade
John Mitchell
2013 - NCT02054832 Canada;
University of Manitoba
2014 - NCT02176096 Canada;
H1 Blocker
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
H2 Blocker
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
MRNA che codifica l’enzima umano deramificante del glicogeno formulato in una nanopaticella lipidica
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
MRNA encoding the human glycogen debranching enzyme formulated in a lipid nanoparticle delivery
Ultragenyx Pharmaceutical Inc.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-ES Canada;France;Germany;Italy;Spain;United Kingdom;United States;
Ramipril
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Sweet polvilho
Hospital de Clinicas de Porto Alegre
2017 - NCT03871673 Brazil;
Tocopherol (vit E)
Dipartimento di Pediatria
2006 - EUCTR2006-005449-12-IT Italy;
Triheptanoin
Areeg El-Gharbawy
2020 Early Phase 1 NCT03665636 United States;
Baylor Research Institute
2009 Phase 2 NCT00947960 France;United States;
UX007
Copenhagen Neuromuscular Center
2018 Phase 2 EUCTR2017-004153-17-DK Denmark;
UX053
ULTRAGENYX PHARMACEUTICAL INC.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-IT Canada;France;Germany;Italy;Spain;United Kingdom;United States;
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04990388 Canada;France;Italy;Spain;United Kingdom;United States;
Ultragenyx Pharmaceutical Inc.
2021 Phase 1;Phase 2 EUCTR2021-000903-19-ES Canada;France;Germany;Italy;Spain;United Kingdom;United States;