TBD

( DrugBank: - / KEGG DRUG: - )


5 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease3
86Pulmonary arterial hypertension3
90Retinitis pigmentosa1
IDDisease name (Link within this page)Number of trials
276Achondroplasia1
299Cystic fibrosis1

19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

86. Pulmonary arterial hypertension


Clinical trials : 1,205Drugs : 684 - (DrugBank : 124) / Drug target genes : 100 - Drug target pathways : 193 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

90. Retinitis pigmentosa


Clinical trials : 147Drugs : 176 - (DrugBank : 43) / Drug target genes : 49 - Drug target pathways : 110 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

276. Achondroplasia


Clinical trials : 51Drugs : 34 - (DrugBank : 6) / Drug target genes : 4 - Drug target pathways : 26 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries