Vatiquinone (DrugBank: Vatiquinone)
2 diseasesID | Disease name (Link within this page) | Number of trials |
---|---|---|
18 | Spinocerebellar degeneration | 1 |
21 | Mitochondrial disease | 1 |
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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1 | NCT04577352 (ClinicalTrials.gov) | November 17, 2020 | 30/9/2020 | A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich Ataxia | A Randomized, Parallel-Arm, Double-Blind, Placebo-Controlled Study With Open-Label Extension to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Friedreich Ataxia (MOVE-FA) | Friedreich Ataxia | Drug: Vatiquinone;Drug: Placebo | PTC Therapeutics | NULL | Not yet recruiting | 7 Years | N/A | All | 126 | Phase 2;Phase 3 | United States;Australia;Canada;Italy |
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT04378075 (ClinicalTrials.gov) | September 28, 2020 | 4/5/2020 | A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsy | Efficacy and Safety Study of Vatiquinone for the Treatment of Mitochondrial Disease Subjects With Refractory Epilepsy | Mitochondrial Diseases;Drug Resistant Epilepsy;Leigh Disease;Leigh Syndrome;Mitochondrial Encephalopathy (MELAS);Pontocerebellar Hypoplasia Type 6 (PCH6);Alpers Disease;Alpers Syndrome | Drug: Vatiquinone;Other: Placebo | PTC Therapeutics | NULL | Recruiting | N/A | 18 Years | All | 60 | Phase 2;Phase 3 | United States |