1 | 291844 | - | - | - | - | [2] 246 246, 299 💬 |
2 | ATALUREN | [1] Ataluren Ataluren | [1] Ataluren
Ataluren
💬 | - | - | [6] 19 19, 113, 140, 246, 299, 329 💬 |
3 | Ataluren 1000mg | [1] Ataluren Ataluren | [1] Ataluren
Ataluren
💬 | - | - | [1] 246 246 💬 |
4 | Ataluren 125mg | [1] Ataluren Ataluren | [1] Ataluren
Ataluren
💬 | - | - | [1] 246 246 💬 |
5 | Ataluren 250mg | [1] Ataluren Ataluren | [1] Ataluren
Ataluren
💬 | - | - | [1] 246 246 💬 |
6 | BBP-671 | - | - | - | - | [2] 245 245, 246 💬 |
7 | Bucladesine | [1] Bucladesine Bucladesine | [1] Bucladesine
Bucladesine
💬 | [16] PDE10A PDE10A, PDE11A, PDE1A, PDE1B, PDE1C, PDE2A, PDE3A, PDE3B, PDE4A, PDE4B, PDE4C, PDE4D, PDE7A, PDE7B, PDE8A, PDE8B 💬 | [18] Aldosterone synthesis and secretion Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Cortisol synthesis and secretion, Cushing syndrome, Glucagon signaling pathway, Insulin signaling pathway, Metabolic pathways, Morphine addiction, Olfactory transduction, Parathyroid hormone synthesis, secretion and action, Progesterone-mediated oocyte maturation, Purine metabolism, Regulation of lipolysis in adipocytes, Renin secretion, Taste transduction, cAMP signaling pathway, cGMP-PKG signaling pathway 💬 | [1] 246 246 💬 |
8 | Carbaglu | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬 | [1] CPS1 CPS1 💬 | [6] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬 | [2] 245 245, 246 💬 |
9 | Carglumic Acid | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬 | [1] CPS1 CPS1 💬 | [6] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬 | [3] 245 245, 246, 251 💬 |
10 | Carglumic Acid (Carbaglu®) | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬 | [1] CPS1 CPS1 💬 | [6] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬 | [2] 245 245, 246 💬 |
11 | Coenzyme A | [1] Coenzyme A Coenzyme A | - | - | - | [1] 246 246 💬 |
12 | Compound 1a | - | - | - | - | [2] 246 246, 299 💬 |
13 | HLB-001 | - | - | - | - | [1] 246 246 💬 |
14 | HST5040 | - | - | - | - | [2] 245 245, 246 💬 |
15 | Methylmalonyl-coenzyme A | [2] (R)-methylmalonyl-CoA (R)-methylmalonyl-CoA, Coenzyme A | - | - | - | [1] 246 246 💬 |
16 | Modified mRNA encoding human methylmalonyl-coenzyme A mutase | [2] (R)-methylmalonyl-CoA (R)-methylmalonyl-CoA, Coenzyme A | - | - | - | [1] 246 246 💬 |
17 | MRNA-3704 | - | - | - | - | [1] 246 246 💬 |
18 | MRNA-3705 | - | - | - | - | [1] 246 246 💬 |
19 | N-Carbamylglutamate | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬 | [1] CPS1 CPS1 💬 | [6] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬 | [2] 245 245, 246 💬 |
20 | None | [1] Interleukin-1 alpha, human recombinant Interleukin-1 alpha, human recombinant | - | - | - | [20] 6 6, 46, 51, 65, 66, 78, 84, 85, 96, 97, 140, 160, 161, 171, 222, 231, 246, 271, 299, 337 💬 |
21 | PEG | - | - | - | - | [15] 6 6, 13, 41, 46, 60, 65, 78, 96, 97, 140, 144, 240, 246, 299, 337 💬 |
22 | PTC-0161480 | - | - | - | - | [2] 246 246, 299 💬 |
23 | PTC-124 | - | - | - | - | [2] 246 246, 299 💬 |
24 | PTC-C124 | - | - | - | - | [2] 246 246, 299 💬 |
25 | PTC124 | - | - | - | - | [4] 19 19, 113, 246, 299 💬 |
26 | RhGH | [1] Somatotropin Somatotropin | - | - | - | [6] 76 76, 78, 96, 193, 246, 337 💬 |
27 | RPS 2505 | - | - | - | - | [2] 246 246, 299 💬 |
28 | Standard of Care Treatment | - | - | - | - | [3] 53 53, 245, 246 💬 |