ACETYLCYSTEINE ( DrugBank: Acetylcysteine )


21 diseases
IDDisease name (Link within this page)Number of trials
6Parkinson disease5
13Multiple sclerosis/Neuromyelitis optica2
19Lysosomal storage disease3
20Adrenoleukodystrophy1
21Mitochondrial disease1
49Systemic lupus erythematosus1
51Scleroderma2
53Sjogren syndrome1
58Hypertrophic cardiomyopathy1
63Idiopathic thrombocytopenic purpura1
85Idiopathic interstitial pneumonia18
90Retinitis pigmentosa4
94Primary sclerosing cholangitis1
111Congenital myopathy1
164Oculocutaneous albinism1
193Prader-Willi syndrome1
233Wolfram syndrome1
296Biliary atresia2
298Hereditary pancreatitis1
299Cystic fibrosis8
337Homocystinuria2

6. Parkinson disease


Clinical trials : 2,307Drugs : 2,007 - (DrugBank : 349) / Drug target genes : 188 - Drug target pathways : 199 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
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agemax
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gender
Target_
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PhaseCountries

13. Multiple sclerosis/Neuromyelitis optica


Clinical trials : 3,340Drugs : 2,163 - (DrugBank : 383) / Drug target genes : 241 - Drug target pathways : 238 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
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agemax
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size
PhaseCountries

19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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20. Adrenoleukodystrophy


Clinical trials : 61Drugs : 90 - (DrugBank : 31) / Drug target genes : 23 - Drug target pathways : 126 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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21. Mitochondrial disease


Clinical trials : 39Drugs : 42 - (DrugBank : 32) / Drug target genes : 47 - Drug target pathways : 67 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
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PhaseCountries

49. Systemic lupus erythematosus


Clinical trials : 993Drugs : 702 - (DrugBank : 184) / Drug target genes : 116 - Drug target pathways : 200 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
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agemax
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size
PhaseCountries

51. Scleroderma


Clinical trials : 525Drugs : 565 - (DrugBank : 148) / Drug target genes : 114 - Drug target pathways : 217 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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agemin
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agemax
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size
PhaseCountries

53. Sjogren syndrome


Clinical trials : 305Drugs : 325 - (DrugBank : 104) / Drug target genes : 58 - Drug target pathways : 188 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
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agemax
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size
PhaseCountries

58. Hypertrophic cardiomyopathy


Clinical trials : 126Drugs : 135 - (DrugBank : 42) / Drug target genes : 46 - Drug target pathways : 162 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
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agemax
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size
PhaseCountries

63. Idiopathic thrombocytopenic purpura


Clinical trials : 391Drugs : 235 - (DrugBank : 50) / Drug target genes : 49 - Drug target pathways : 139 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
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agemax
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Target_
size
PhaseCountries

85. Idiopathic interstitial pneumonia


Clinical trials : 627Drugs : 443 - (DrugBank : 120) / Drug target genes : 99 - Drug target pathways : 212 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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agemax
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PhaseCountries

90. Retinitis pigmentosa


Clinical trials : 147Drugs : 176 - (DrugBank : 43) / Drug target genes : 49 - Drug target pathways : 110 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
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agemin
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PhaseCountries

94. Primary sclerosing cholangitis


Clinical trials : 148Drugs : 118 - (DrugBank : 39) / Drug target genes : 18 - Drug target pathways : 141 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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agemin
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agemax
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PhaseCountries

111. Congenital myopathy


Clinical trials : 10Drugs : 17 - (DrugBank : 5) / Drug target gene : 1 - Drug target pathways : 9 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
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agemin
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agemax
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size
PhaseCountries

164. Oculocutaneous albinism


Clinical trials : 15Drugs : 54 - (DrugBank : 34) / Drug target genes : 35 - Drug target pathways : 141 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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agemax
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193. Prader-Willi syndrome


Clinical trials : 113Drugs : 111 - (DrugBank : 26) / Drug target genes : 48 - Drug target pathways : 102 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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agemax
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size
PhaseCountries

233. Wolfram syndrome


Clinical trials : 11Drugs : 17 - (DrugBank : 8) / Drug target genes : 12 - Drug target pathways : 41 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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agemax
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PhaseCountries

296. Biliary atresia


Clinical trials : 71Drugs : 70 - (DrugBank : 39) / Drug target genes : 35 - Drug target pathways : 60 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
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agemax
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size
PhaseCountries

298. Hereditary pancreatitis


Clinical trials : 95Drugs : 148 - (DrugBank : 51) / Drug target genes : 53 - Drug target pathways : 142 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
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agemax
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gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
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agemax
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gender
Target_
size
PhaseCountries

337. Homocystinuria


Clinical trials : 16Drugs : 19 - (DrugBank : 7) / Drug target genes : 2 - Drug target pathways : 23 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries