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597 / 17,542 descriptions

No. Drug (Description in trials) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY
On map, Yellow: Drug target genes		 Disease ID
 1  1- deoxygalactonojirimycin  -  -  -  -  [1] 19 💬 
 2  1-deoxygalactonojirimycin  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 3  1-deoxygalactonojirimycin hydrochloride  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 4  12s-it  -  -  -  -  [1] 19 💬 
 5  15 o water  Water  [1] D00001 💬  -  -  [1] 19 💬 
 6  2(s)-(acetylamino)-4-methylpentanoic acid  -  -  -  -  [1] 19 💬 
 7  2-aminoethanethiol  Cysteamine  [2] D03634, D03635 💬  -  -  [2] 19, 299 💬 
 8  2-hydroxypropyl-beta-cyclodextrin  Betadex  [1] D02401 💬  -  -  [1] 19 💬 
 9  4d-310  -  -  -  -  [1] 19 💬 
 10  500 0500 0  -  -  -  -  [1] 19 💬 
 11  89 zirconium recombinant human alpha-n-acetylglucosaminidase (rhnaglu) (radiolabeled)  -  -  -  -  [1] 19 💬 
 12  89zr-sbc-103  -  -  -  -  [1] 19 💬 
 13  [045251016]  -  -  -  -  [1] 19 💬 
 14  [14c] at1001  -  -  -  -  [1] 19 💬 
 15  [a16ab04]  -  -  -  -  [1] 19 💬 
 16  [at1001]  -  -  -  -  [1] 19 💬 
 17  [hgt-1410]  -  -  -  -  [1] 19 💬 
 18  [otl-200]  -  -  -  -  [1] 19 💬 
 19  [rhlaman]  Velmanase alfa  [1] D11024 💬  [1] MAN2B1 💬  [2] Lysosome, Other glycan degradation  [1] 19 💬 
 20  [shp611]  -  -  -  -  [1] 19 💬 
 21  A (migalastat)  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 22  A16ab04  -  -  -  -  [1] 19 💬 
 23  A16ax06  -  -  -  -  [1] 19 💬 
 24  Aav2/8.tbg.harsb  -  -  -  -  [1] 19 💬 
 25  Aav2cuhcln2 (3x10^12 particle units)  -  -  -  -  [1] 19 💬 
 26  Aav9-cag-coh-sgsh  -  -  -  -  [1] 19 💬 
 27  Aav9-glb1  -  -  -  -  [1] 19 💬 
 28  Aavrh.10-hmpsiiia  -  -  -  -  [1] 19 💬 
 29  Aavrh.10cuarsa  -  -  -  -  [1] 19 💬 
 30  Aavrh.10cucln2  -  -  -  -  [1] 19 💬 
 31  Aavrh.10cuhcln2 vector 2.85x10^11 genome copies  -  -  -  -  [1] 19 💬 
 32  Aavrh.10cuhcln2 vector 9.0x10^11 genome copies  -  -  -  -  [1] 19 💬 
 33  Abatacept  Abatacept  [1] D03203 💬  [2] CD80, CD86 💬  [12] Allograft rejection, Autoimmune thyroid disease, Cell adhesion molecules, Graft-versus-host disease, Intestinal immune network for IgA production, Kaposi sarcoma-associated herpesvirus infection, Rheumatoid arthritis, Systemic lupus erythematosus, Toll-like receptor signaling pathway, Transcriptional misregulation in cancer, Type I diabetes mellitus, Viral myocarditis  [26] 11, 13, 19, 41, 44, 46, 49, 50, 51, 53, 55, 60, 65, 84, 93, 95, 96, 97, 107, 160, 164, 222, 271, 284, 285, 300 💬 
 34  Abo-101  -  -  -  -  [1] 19 💬 
 35  Abo-102  -  -  -  -  [1] 19 💬 
 36  Accupro  -  -  -  -  [1] 19 💬 
 37  Accuretic  -  -  -  -  [1] 19 💬 
 38  Acetylcysteine  Acetylcysteine  [1] D00221 💬  -  -  [16]  6 , 13, 19, 20, 34, 49, 51, 58, 85, 94, 111, 164, 193, 233, 298, 299 💬 
 39  Act-434964  -  -  -  -  [1] 19 💬 
 40  Adalimumab  Adalimumab  [1] D02597 💬  [1] TNF 💬  [65] AGE-RAGE signaling pathway in diabetic complications, Adipocytokine signaling pathway, African trypanosomiasis, Allograft rejection, Alzheimer disease, Amoebiasis, Amyotrophic lateral sclerosis, Antifolate resistance, Antigen processing and presentation, Apoptosis, Asthma, C-type lectin receptor signaling pathway, Chagas disease, Coronavirus disease - COVID-19, Cytokine-cytokine receptor interaction, Dilated cardiomyopathy, Epstein-Barr virus infection, Fc epsilon RI signaling pathway, Fluid shear stress and atherosclerosis, Graft-versus-host disease, Hematopoietic cell lineage, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, Hypertrophic cardiomyopathy, IL-17 signaling pathway, Inflammatory bowel disease, Influenza A, Insulin resistance, Legionellosis, Leishmaniasis, MAPK signaling pathway, Malaria, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Natural killer cell mediated cytotoxicity, Necroptosis, Non-alcoholic fatty liver disease, Osteoclast differentiation, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Prion disease, Proteoglycans in cancer, RIG-I-like receptor signaling pathway, Rheumatoid arthritis, Salmonella infection, Shigellosis, Sphingolipid signaling pathway, Systemic lupus erythematosus, T cell receptor signaling pathway, TGF-beta signaling pathway, TNF signaling pathway, Toll-like receptor signaling pathway, Toxoplasmosis, Tuberculosis, Type I diabetes mellitus, Type II diabetes mellitus, Viral protein interaction with cytokine and cytokine receptor, Yersinia infection, mTOR signaling pathway  [16] 19, 37, 40, 41, 46, 56, 84, 96, 97, 151, 160, 164, 222, 226, 269, 271 💬 
 41  Adalimumab injection [humira]  Adalimumab  [1] D02597 💬  [1] TNF 💬  [65] AGE-RAGE signaling pathway in diabetic complications, Adipocytokine signaling pathway, African trypanosomiasis, Allograft rejection, Alzheimer disease, Amoebiasis, Amyotrophic lateral sclerosis, Antifolate resistance, Antigen processing and presentation, Apoptosis, Asthma, C-type lectin receptor signaling pathway, Chagas disease, Coronavirus disease - COVID-19, Cytokine-cytokine receptor interaction, Dilated cardiomyopathy, Epstein-Barr virus infection, Fc epsilon RI signaling pathway, Fluid shear stress and atherosclerosis, Graft-versus-host disease, Hematopoietic cell lineage, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, Hypertrophic cardiomyopathy, IL-17 signaling pathway, Inflammatory bowel disease, Influenza A, Insulin resistance, Legionellosis, Leishmaniasis, MAPK signaling pathway, Malaria, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Natural killer cell mediated cytotoxicity, Necroptosis, Non-alcoholic fatty liver disease, Osteoclast differentiation, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Prion disease, Proteoglycans in cancer, RIG-I-like receptor signaling pathway, Rheumatoid arthritis, Salmonella infection, Shigellosis, Sphingolipid signaling pathway, Systemic lupus erythematosus, T cell receptor signaling pathway, TGF-beta signaling pathway, TNF signaling pathway, Toll-like receptor signaling pathway, Toxoplasmosis, Tuberculosis, Type I diabetes mellitus, Type II diabetes mellitus, Viral protein interaction with cytokine and cytokine receptor, Yersinia infection, mTOR signaling pathway  [1] 19 💬 
 42  Adeno-associated viral (aav) serotype 8 (aav2/8) vector with liver-specific thyroxine-binding globulin (tbg) promoter, driving the expression of the human arsb gene  Levothyroxine  [2] D01010, D08125 💬  [2] THRA, THRB 💬  [2] Neuroactive ligand-receptor interaction, Thyroid hormone signaling pathway  [1] 19 💬 
 43  Adeno-associated viral vector serotype 9 containing the human n-acetyl-alpha-glucosaminidase gene  -  -  -  -  [1] 19 💬 
 44  Adeno-associated virus serotype 2/6 encoding human alpha-galactosidase a cdna  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 45  Adeno-associated virus serotype 2/6 encoding human iduronate 2-sulfatase (hids) gene donor vector, sb-a6p-hnt donor vector  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 46  Adeno-associated virus serotype 2/6 encoding human iduronidase (hidua) gene donor vector, sb-a6p-hrl donor vector  -  -  -  -  [1] 19 💬 
 47  Adeno-associated virus serotype 2/6 encoding left side-zinc finger nuclease (zfn1), sb-a6p-zleft vector  -  -  -  -  [1] 19 💬 
 48  Adeno-associated virus serotype 2/6 encoding right side-zinc finger nuclease (zfn2), sb-a6p-zright vector  -  -  -  -  [1] 19 💬 
 49  Administration  -  -  -  -  [1] 19 💬 
 50  Adrabetadex  Adrabetadex  -  -  -  [1] 19 💬 
 51  Afegostat  Afegostat  [1] D09576 💬  -  -  [1] 19 💬 
 52  Afegostat tartrate  Afegostat  [1] D09576 💬  -  -  [1] 19 💬 
 53  Agalsidase  -  -  -  -  [1] 19 💬 
 54  Agalsidase alfa  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 55  Agalsidase alpha  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 56  Agalsidase beta  Agalsidase beta  [1] D03228 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 57  Agalsidase beta (gz419828)  Agalsidase beta  [1] D03228 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 58  Agalsidase beta (recombinant form)  Agalsidase beta  [1] D03228 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 59  Agalsidasi beta  -  -  -  -  [1] 19 💬 
 60  Agt-181  -  -  -  -  [1] 19 💬 
 61  Agt-181 (hirmab-idua)  -  -  -  -  [1] 19 💬 
 62  Agt-182  -  -  -  -  [1] 19 💬 
 63  Aldurazyme  -  -  -  -  [1] 19 💬 
 64  Aldurazyme (laronidase)  Laronidase  [1] D04670 💬  [1] IDUA 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [2] 19, 256 💬 
 65  Aldurazyme (recombinant human alpha-l-iduronidase)  -  -  -  -  [1] 19 💬 
 66  Aldurazyme*infus 1fl 5ml 500u  -  -  -  -  [1] 19 💬 
 67  Alemtuzumab  Alemtuzumab  [1] D02802 💬  -  -  [16] 13, 15, 19, 20, 43, 44, 46, 51, 60, 63, 65, 85, 96, 164, 283, 284 💬 
 68  Alendronate  Alendronic acid  [2] D00939, D07119 💬  [1] FDPS 💬  [4] Human T-cell leukemia virus 1 infection, Influenza A, Metabolic pathways, Terpenoid backbone biosynthesis  [7] 19, 41, 46, 50, 271, 274, 299 💬 
 69  Alendronate sodium  Alendronic acid  [2] D00939, D07119 💬  [1] FDPS 💬  [4] Human T-cell leukemia virus 1 infection, Influenza A, Metabolic pathways, Terpenoid backbone biosynthesis  [2] 19, 299 💬 
 70  Alfa-manosidadas humana recombinante  -  -  -  -  [1] 19 💬 
 71  Alpha-galactosidase a  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 72  Ambroxol  Ambroxol  [1] D07442 💬  -  -  [2]  6 , 19 💬 
 73  Anakinra  Anakinra  [1] D02934 💬  [2] IL1R1, IL1R2 💬  [15] Amoebiasis, Cytokine-cytokine receptor interaction, Fluid shear stress and atherosclerosis, Hematopoietic cell lineage, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Inflammatory mediator regulation of TRP channels, MAPK signaling pathway, NF-kappa B signaling pathway, Osteoclast differentiation, Pathogenic Escherichia coli infection, Prostate cancer, Shigellosis, Th17 cell differentiation, Transcriptional misregulation in cancer  [17]  2 , 13, 15, 19, 28, 37, 41, 46, 49, 50, 56, 84, 86, 97, 106, 107, 299 💬 
 74  Angiotensin  Angiotensin II  [2] D00150, D02014 💬  [2] AGTR1, AGTR2 💬  [16] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway  [7] 17, 19, 46, 66, 86, 222, 224 💬 
 75  Arimoclomol  Arimoclomol  [1] D11374 💬  -  -  [3]  2 , 15, 19 💬 
 76  Arimoclomol (hard gelatine capsule)  Arimoclomol  [3] D00115, D06892, D11374 💬  -  -  [1] 19 💬 
 77  Arimoclomol (hpmc capsule)  Arimoclomol  [1] D11374 💬  -  -  [1] 19 💬 
 78  Arimoclomol citrate  Arimoclomol  [1] D11374 💬  -  -  [2] 15, 19 💬 
 79  Arylsulfatase a  -  -  -  -  [1] 19 💬 
 80  At1001  -  -  -  -  [1] 19 💬 
 81  At1001 150 mg  -  -  -  -  [1] 19 💬 
 82  At2101  -  -  -  -  [1] 19 💬 
 83  Ataluren  Ataluren  [1] D09323 💬  -  -  [6] 19, 113, 140, 246, 299, 329 💬 
 84  Autologous cd34+ cells transduced with a lentiviral vector containing the human sgsh gene  -  -  -  -  [1] 19 💬 
 85  Autologous cd34+ cells transduced with a lentiviral vector encoding the arsa cdna  -  -  -  -  [1] 19 💬 
 86  Autologous plasmablasts  -  -  -  -  [1] 19 💬 
 87  Avr-rd-01  -  -  -  -  [1] 19 💬 
 88  Avr-rd-02  -  -  -  -  [1] 19 💬 
 89  Ax  -  -  -  -  [1] 19 💬 
 90  Ax 250  -  -  -  -  [1] 19 💬 
 91  Azathioprine  Azathioprine  [2] D00238, D03033 💬  -  -  [20]  6 , 11, 13, 19, 35, 42, 43, 44, 45, 46, 49, 63, 65, 66, 85, 94, 95, 96, 97, 162 💬 
 92  Azathioprine (aza)  Azathioprine  [2] D00238, D03033 💬  -  -  [3] 13, 19, 97 💬 
 93  B (migalastat)  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 94  Barium  Barium  -  -  -  [2] 19, 98 💬 
 95  Behavioral: neurocognitive testing  -  -  -  -  [1] 19 💬 
 96  Behavioral: picc line placement  -  -  -  -  [1] 19 💬 
 97  Beta-cyclodextrin  Betadex  [1] D02401 💬  -  -  [1] 19 💬 
 98  Beta-mercaptoethylamine  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 99  Beta-mercaptoethylamine hydrochloride & 2-aminoethanethiol hydrochloride  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 100  Bhp001  -  -  -  -  [1] 19 💬 
 101  Biological assays  -  -  -  -  [1] 19 💬 
 102  Biopsy  -  -  -  -  [2] 19, 51 💬 
 103  Blood sampling  -  -  -  -  [5] 13, 17, 19, 51, 96 💬 
 104  Bm110  -  -  -  -  [1] 19 💬 
 105  Bmn 110  -  -  -  -  [1] 19 💬 
 106  Bmn 110 - every other week  -  -  -  -  [1] 19 💬 
 107  Bmn 110 - weekly  -  -  -  -  [1] 19 💬 
 108  Bmn 110 every other week  -  -  -  -  [1] 19 💬 
 109  Bmn 110 weekly  -  -  -  -  [1] 19 💬 
 110  Bmn 190  -  -  -  -  [1] 19 💬 
 111  Bmn 250  -  -  -  -  [1] 19 💬 
 112  Bmn190 recombinant human tripeptidyl peptidase-1 (rhtpp1)  -  -  -  -  [1] 19 💬 
 113  Brineura  -  -  -  -  [1] 19 💬 
 114  Busilvex  -  -  -  -  [4] 19, 36, 60, 65 💬 
 115  Busilvex - 6 mg/ml - concentrato per soluzione per infusione - uso endovenoso - flaconcino - 10 ml 8 flaconcini  -  -  -  -  [2] 19, 65 💬 
 116  Busulfan  Busulfan  [1] D00248 💬  -  -  [13] 19, 20, 28, 36, 49, 51, 60, 65, 164, 274, 284, 285, 326 💬 
 117  Busulfan, cyclophosphamide, antithymocyte globulin  Busulfan  [3] D00248, D00287, D07760 💬  -  -  [2] 19, 20 💬 
 118  Busulfan, cyclophosphamide, atg  Busulfan  [3] D00248, D00287, D07760 💬  -  -  [1] 19 💬 
 119  Busulfano  Busulfan  [1] D00248 💬  -  -  [1] 19 💬 
 120  C (migalastat)  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 121  Calcium  Calcium  -  -  -  [27]  6 , 13, 19, 46, 49, 51, 53, 56, 68, 75, 79, 84, 93, 94, 95, 96, 97, 186, 214, 215, 222, 224, 235, 265, 274, 298, 299 💬 
 122  Calcium carbonate  Calcium  [2] D00932, D10802 💬  -  -  [8] 13, 19, 46, 53, 75, 96, 235, 299 💬 
 123  Cald hr-d (high-risk, regimen c)  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 124  Cald hr-d (high-risk, regimen d)  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 125  Cald sr-a (standard-risk, regimen a)  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 126  Cald sr-b (standard-risk, regimen b)  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 127  Campath  -  -  -  -  [12] 19, 20, 49, 51, 60, 62, 65, 164, 234, 283, 285, 326 💬 
 128  Campath-1h  -  -  -  -  [6] 19, 20, 60, 234, 285, 326 💬 
 129  Capsaicin  Capsaicin  [1] D00250 💬  [1] TRPV1 💬  [2] Inflammatory mediator regulation of TRP channels, Neuroactive ligand-receptor interaction  [5]  2 ,  6 , 19, 86, 226 💬 
 130  Carbonate  Carbonate ion  -  -  -  [12]  2 , 13, 17, 18, 19, 46, 53, 75, 96, 127, 235, 299 💬 
 131  Cellule cd34+ autologhe trasdotte con idua lv codificante per il cdna dell'alfa-l-iduronidasi  -  -  -  -  [1] 19 💬 
 132  Cerdelga  -  -  -  -  [1] 19 💬 
 133  Ceredase  -  -  -  -  [1] 19 💬 
 134  Ceredase™  -  -  -  -  [1] 19 💬 
 135  Cerezyme  -  -  -  -  [1] 19 💬 
 136  Cerezyme (imiglucerase for injection)  Imiglucerase  [2] D02810, D03020 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 137  Cerezyme®  -  -  -  -  [1] 19 💬 
 138  Cerezyme® / imiglucerase  Imiglucerase  [2] D02810, D03020 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 139  Cerliponase alfa  Cerliponase alfa  [1] D10813 💬  [1] TPP1 💬  [1] Lysosome  [1] 19 💬 
 140  Chemically modified recombinant human sulfamidase  -  -  -  -  [1] 19 💬 
 141  Cholecalciferol  Cholecalciferol  [1] D00188 💬  [1] VDR 💬  [4] Endocrine and other factor-regulated calcium reabsorption, Mineral absorption, Parathyroid hormone synthesis, secretion and action, Tuberculosis  [9] 13, 19, 34, 46, 49, 96, 97, 298, 299 💬 
 142  Cholesterol  Cholesterol  [1] D00040 💬  -  -  [6] 19, 90, 160, 259, 261, 310 💬 
 143  Clofarabine  Clofarabine  [1] D03546 💬  [3] POLA1, POLA2, RRM1 💬  [6] DNA replication, Drug metabolism - other enzymes, Glutathione metabolism, Metabolic pathways, Purine metabolism, Pyrimidine metabolism  [9] 19, 20, 40, 46, 49, 60, 96, 234, 326 💬 
 144  Coversyl  -  -  -  -  [2] 19, 167 💬 
 145  Coversyl plus  -  -  -  -  [1] 19 💬 
 146  Cryopreserved autologous cd34+ cells transduced with a lentiviral vector containing human sgsh gene  -  -  -  -  [1] 19 💬 
 147  Csa  -  -  -  -  [8] 19, 49, 50, 53, 60, 63, 222, 228 💬 
 148  Cyclophosphamide  Cyclophosphamide  [2] D00287, D07760 💬  -  -  [44] 11, 13, 14, 16, 19, 20, 26, 28, 35, 36, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 52, 56, 60, 62, 65, 66, 84, 85, 93, 96, 162, 164, 172, 222, 224, 256, 265, 274, 283, 284, 285, 288, 326, 331 💬 
 149  Cyclosporine  Cyclosporine  [1] D00184 💬  [5] PPP3CA, PPP3CB, PPP3CC, PPP3R1, PPP3R2 💬  [32] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway  [35] 11, 19, 20, 28, 36, 38, 39, 40, 41, 42, 45, 46, 49, 50, 53, 56, 58, 60, 62, 63, 64, 65, 90, 95, 97, 162, 164, 222, 226, 228, 234, 283, 284, 285, 302 💬 
 150  Cyclosporine a  Cyclosporine  [1] D00184 💬  [5] PPP3CA, PPP3CB, PPP3CC, PPP3R1, PPP3R2 💬  [32] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway  [10] 19, 20, 36, 49, 50, 53, 58, 60, 234, 283 💬 
 151  Cyclosporine a (csa)  Cyclosporine  [1] D00184 💬  [5] PPP3CA, PPP3CB, PPP3CC, PPP3R1, PPP3R2 💬  [32] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway  [2] 19, 60 💬 
 152  Cystadane anhydrous  -  -  -  -  [1] 19 💬 
 153  Cystadrops  -  -  -  -  [1] 19 💬 
 154  Cystadrops 0.55% eye drops, solution  -  -  -  -  [1] 19 💬 
 155  Cystagon  -  -  -  -  [3]  8 , 19, 299 💬 
 156  Cystagon 150mg  -  -  -  -  [1] 19 💬 
 157  Cystagon 50mg  -  -  -  -  [1] 19 💬 
 158  Cystagon®  -  -  -  -  [1] 19 💬 
 159  Cystagon® (cysteamine bitartrate)  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 160  Cysteamine  Cysteamine  [2] D03634, D03635 💬  -  -  [4]  8 , 19, 21, 299 💬 
 161  Cysteamine (mercaptamine) viscous solution  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 162  Cysteamine bitartrate  Cysteamine  [2] D03634, D03635 💬  -  -  [4]  8 , 19, 21, 299 💬 
 163  Cysteamine bitartrate (inn: mercaptamine bitartrate  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 164  Cysteamine bitartrate (inn: mercaptamine bitartrate )  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 165  Cysteamine bitartrate (inn: mercaptamine bitartrate)  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 166  Cysteamine bitartrate delayed-release capsules  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 167  Cysteamine bitartrate delayed-release capsules (rp103)  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 168  Cysteamine hydrochloride  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 169  Cysteine  Cysteine  [2] D00026, D02326 💬  -  -  [11]  6 , 13, 19, 34, 84, 85, 88, 90, 254, 296, 310 💬 
 170  D (migalastat)  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 171  Device: administration kit  -  -  -  -  [1] 19 💬 
 172  Device: cyclosporine a  Cyclosporine  [1] D00184 💬  [5] PPP3CA, PPP3CB, PPP3CC, PPP3R1, PPP3R2 💬  [32] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway  [2] 19, 20 💬 
 173  Device: intraventricular access device  -  -  -  -  [1] 19 💬 
 174  Device: mechanical stimulation with von frey filaments  -  -  -  -  [1] 19 💬 
 175  Device: mri with contrast agent injection  -  -  -  -  [1] 19 💬 
 176  Device: mri without contrast agent injection  -  -  -  -  [1] 19 💬 
 177  Device: osome  -  -  -  -  [1] 19 💬 
 178  Device: temperature sensitivity measurement with advanced thermal stimulation  -  -  -  -  [1] 19 💬 
 179  Diagnostic test: audiology assessmentwith abr  -  -  -  -  [1] 19 💬 
 180  Diagnostic test: bone density scan (dexa  -  -  -  -  [1] 19 💬 
 181  Diagnostic test: echocardiogram  -  -  -  -  [1] 19 💬 
 182  Diagnostic test: echocardiography at m24  -  -  -  -  [1] 19 💬 
 183  Diagnostic test: echocardiography at t0  -  -  -  -  [1] 19 💬 
 184  Diagnostic test: electrocardiogram (ekg)  -  -  -  -  [1] 19 💬 
 185  Diagnostic test: exercise test  -  -  -  -  [1] 19 💬 
 186  Diagnostic test: laboratory tests  -  -  -  -  [1] 19 💬 
 187  Dnl310  -  -  -  -  [1] 19 💬 
 188  Dnl310 drug substance  -  -  -  -  [1] 19 💬 
 189  Dried blood spot (dbs) sampling  -  -  -  -  [1] 19 💬 
 190  Drx005b  -  -  -  -  [1] 19 💬 
 191  Duoc-01  -  -  -  -  [2] 19, 20 💬 
 192  E (migalastat)  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 193  Elaprase  -  -  -  -  [1] 19 💬 
 194  Elaprase 2mg/ml  -  -  -  -  [1] 19 💬 
 195  Elaprase for intravenous (iv) infusion  -  -  -  -  [1] 19 💬 
 196  Elaprase_0.5mg/kg  -  -  -  -  [1] 19 💬 
 197  Elelyso  -  -  -  -  [1] 19 💬 
 198  Elelyso 60 units/kg  -  -  -  -  [1] 19 💬 
 199  Eliglustat  Eliglustat  [1] D09893 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 200  Eliglustat gz385660  Eliglustat  [1] D09893 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 201  Eliglustat tartrate  Eliglustat  [1] D09893 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 202  Elosulfase alfa  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 203  Elosulfase alfa 1 mg/ml intravenous solution [vimizim]  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 204  Elx-02  ELX-02  -  -  -  [2] 19, 299 💬 
 205  Enalapril  Enalapril  [2] D00621, D07892 💬  [1] ACE 💬  [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system  [7] 19, 46, 66, 113, 210, 222, 223 💬 
 206  Enalapril and other angiotensin converting enzyme inhibitors  Angiotensin II  [4] D00150, D00621, D02014, D07892 💬  [3] ACE, AGTR1, AGTR2 💬  [18] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Chagas disease, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway  [1] 19 💬 
 207  Enriched hematopoetic stem cell infusion  -  -  -  -  [3] 13, 19, 284 💬 
 208  Enzyme replacement  -  -  -  -  [1] 19 💬 
 209  Enzyme replacement therapy  -  -  -  -  [1] 19 💬 
 210  Enzyme replacement therapy (agalsidase alpha (replagal®))  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 211  Enzyme replacement therapy (ert)  -  -  -  -  [1] 19 💬 
 212  Ert  -  -  -  -  [1] 19 💬 
 213  Fabrazyme  -  -  -  -  [1] 19 💬 
 214  Fabrazyme (agalsidase beta)  Agalsidase beta  [1] D03228 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 215  Fabrazyme - 35 mg polvere per concentrato per soluzione per infusione endovenosa 1 flaconcino  -  -  -  -  [1] 19 💬 
 216  Fabrazyme 35 mg  -  -  -  -  [1] 19 💬 
 217  Fabrazyme 5 mg  -  -  -  -  [1] 19 💬 
 218  Flt190  -  -  -  -  [1] 19 💬 
 219  Fludarabina  Fludarabine  [2] D01907, D07966 💬  [1] RRM1 💬  [5] Drug metabolism - other enzymes, Glutathione metabolism, Metabolic pathways, Purine metabolism, Pyrimidine metabolism  [2] 19, 65 💬 
 220  Fludarabina accord - 25 mg/ml concentrato per soluzione iniettabile o per infusione 5 flaconcini in vetro da 2 ml  Fludarabine  [2] D01907, D07966 💬  [1] RRM1 💬  [5] Drug metabolism - other enzymes, Glutathione metabolism, Metabolic pathways, Purine metabolism, Pyrimidine metabolism  [1] 19 💬 
 221  Fludarabina fosfato  Fludarabine  [2] D01907, D07966 💬  [1] RRM1 💬  [5] Drug metabolism - other enzymes, Glutathione metabolism, Metabolic pathways, Purine metabolism, Pyrimidine metabolism  [1] 19 💬 
 222  Fluorescein  Fluorescein  [2] D01261, D02024 💬  -  -  [2] 19, 97 💬 
 223  Ga-gcb  Velaglucerase alfa  [1] D09029 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 224  Ga-gcb (velaglucerase alfa)  Velaglucerase alfa  [1] D09029 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 225  Gabapentin  Gabapentin  [1] D00332 💬  [5] CACNA2D1, CACNA2D2, CACNA2D3, CACNA2D4, SLC6A1 💬  [9] Adrenergic signaling in cardiomyocytes, Arrhythmogenic right ventricular cardiomyopathy, Cardiac muscle contraction, Dilated cardiomyopathy, GABAergic synapse, Hypertrophic cardiomyopathy, MAPK signaling pathway, Oxytocin signaling pathway, Synaptic vesicle cycle  [5]  6 , 13, 19, 70, 298 💬 
 226  Galafold  -  -  -  -  [1] 19 💬 
 227  Galsulfase  Galsulfase  [1] D06565 💬  [1] ARSB 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 228  Gc1111_0.5mg/kg  -  -  -  -  [1] 19 💬 
 229  Gc1111_1.0mg/kg  -  -  -  -  [1] 19 💬 
 230  Gc1119  -  -  -  -  [1] 19 💬 
 231  Gelatine  Gelatin  [2] D00115, D06892 💬  -  -  [1] 19 💬 
 232  Gene activated human glucocerebrosidase  -  -  -  -  [1] 19 💬 
 233  Gene activated human glucocerebrosidase, velaglucerase alfa  Velaglucerase alfa  [1] D09029 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 234  Gene-activated human glucocerebrosidase  -  -  -  -  [1] 19 💬 
 235  Gene-activated human glucocerebrosidase 200u/vial  -  -  -  -  [1] 19 💬 
 236  Gene-activated human glucocerebrosidase 400u/vial  -  -  -  -  [1] 19 💬 
 237  Genetic: gla gene  -  -  -  -  [1] 19 💬 
 238  Genetic: lys-gm101  -  -  -  -  [1] 19 💬 
 239  Genistein  Genistein  [1] D11680 💬  -  -  [2] 19, 299 💬 
 240  Genistein aglycone  Genistein  [1] D11680 💬  -  -  [1] 19 💬 
 241  Genz-112638  -  -  -  -  [1] 19 💬 
 242  Genz-682452  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [3]  6 , 19, 67 💬 
 243  Genz-682452-aa  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 244  Genz-682452-au  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [3]  6 , 19, 67 💬 
 245  Gla  -  -  -  -  [2] 13, 19 💬 
 246  Glucocerebrosidase  -  -  -  -  [1] 19 💬 
 247  Glucocerebrosidase umano gene-attivato  -  -  -  -  [1] 19 💬 
 248  Gnr-055  -  -  -  -  [1] 19 💬 
 249  Gr181413  -  -  -  -  [1] 19 💬 
 250  Gr181413a  -  -  -  -  [1] 19 💬 
 251  Gr181413a/at1001 capsule  -  -  -  -  [1] 19 💬 
 252  Gr181413a/at1001 solution  -  -  -  -  [1] 19 💬 
 253  Growth hormone  Somatotropin  [1] D02691 💬  [1] GHR 💬  [5] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway  [12]  2 , 13, 19, 46, 78, 96, 187, 191, 193, 195, 265, 299 💬 
 254  Gsk2788723  -  -  -  -  [1] 19 💬 
 255  Gz/sar402671  -  -  -  -  [2]  6 , 19 💬 
 256  Gz385660  -  -  -  -  [1] 19 💬 
 257  Gz402665  -  -  -  -  [1] 19 💬 
 258  Gz402671  -  -  -  -  [2] 19, 67 💬 
 259  Gz402671 / sar402671  -  -  -  -  [1] 19 💬 
 260  Hematopoetic stem cell transplantation  -  -  -  -  [5] 19, 65, 120, 160, 326 💬 
 261  Hematopoietic stem cell infusion  -  -  -  -  [2] 19, 20 💬 
 262  Hematopoietic stem cell transplantation  -  -  -  -  [12] 11, 13, 14, 19, 20, 35, 46, 49, 51, 96, 234, 285 💬 
 263  Heparán n sulfatasa humana recombinante  -  -  -  -  [1] 19 💬 
 264  Heparán n sulfatasa humana recombinante (rhhns)  -  -  -  -  [1] 19 💬 
 265  Hgt-1110  -  -  -  -  [1] 19 💬 
 266  Hgt-1111  -  -  -  -  [1] 19 💬 
 267  Hgt-1410  -  -  -  -  [1] 19 💬 
 268  Hgt-2310  -  -  -  -  [1] 19 💬 
 269  Hids donor  -  -  -  -  [1] 19 💬 
 270  Hucns-sc  -  -  -  -  [1] 19 💬 
 271  Human glucocerebrosidase (prgcd)  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 272  Human placental derived stem cell  -  -  -  -  [4] 19, 20, 60, 284 💬 
 273  Hunterase  Idursulfase beta  [1] D11025 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 274  Hydroxypropyl-beta-cyclodextrin  Betadex  [1] D02401 💬  -  -  [1] 19 💬 
 275  Hydroxypropyl-ß-cyclodextrin  -  -  -  -  [1] 19 💬 
 276  Hydroxyurea  Hydroxyurea  [1] D00341 💬  [1] RRM2 💬  [6] Drug metabolism - other enzymes, Glutathione metabolism, Metabolic pathways, Purine metabolism, Pyrimidine metabolism, p53 signaling pathway  [8]  3 , 13, 19, 20, 65, 85, 86, 284 💬 
 277  I2s  -  -  -  -  [1] 19 💬 
 278  I2s-it  -  -  -  -  [1] 19 💬 
 279  Ib1001  -  -  -  -  [1] 19 💬 
 280  Iduronate 2-sulfatase  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 281  Iduronate-2-sulfatase enzyme replacement therapy  -  -  -  -  [1] 19 💬 
 282  Iduronate-2-sulfatase fused to a fc polypeptide that binds to the human transferrin receptor  -  -  -  -  [1] 19 💬 
 283  Idursulfasa  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 284  Idursulfase  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 285  Idursulfase (i2s)  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 286  Idursulfase (i2s)-it  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 287  Idursulfase beta  Idursulfase  [2] D04499, D11025 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 288  Idursulfase it (1 mg)  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 289  Idursulfase it (10 mg)  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 290  Idursulfase it (30 mg)  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 291  Idursulfase(12s)-it  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 292  Idursulfase(i2s)-it  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 293  Idursulfase-it  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 294  Igf2  -  -  -  -  [1] 19 💬 
 295  Imd  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 296  Imd preparative regimen  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 297  Imiglucerasa  Imiglucerase  [2] D02810, D03020 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 298  Imiglucerase  Imiglucerase  [2] D02810, D03020 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 299  Imiglucerase gz437843  Imiglucerase  [2] D02810, D03020 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 300  Imiglucerasi  -  -  -  -  [1] 19 💬 
 301  Imiglucérase (drug) pharmacokinetics  -  -  -  -  [1] 19 💬 
 302  Inactive reminder capsules  -  -  -  -  [1] 19 💬 
 303  Inactive reminder product  -  -  -  -  [1] 19 💬 
 304  Inn not available  -  -  -  -  [2] 19, 46 💬 
 305  Innozide  -  -  -  -  [1] 19 💬 
 306  Intrathecal recombinant human alpha iduronidase  -  -  -  -  [1] 19 💬 
 307  Iohexol  Iohexol  [1] D01817 💬  -  -  [2] 19, 67 💬 
 308  Irt laronidase  Laronidase  [1] D04670 💬  [1] IDUA 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 309  Isofagamine tartrate  -  -  -  -  [1] 19 💬 
 310  Isu302  -  -  -  -  [1] 19 💬 
 311  Iv migalastat hcl  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 312  Iva 336  -  -  -  -  [1] 19 💬 
 313  Jr-141  -  -  -  -  [1] 19 💬 
 314  Jr-141 or idursulfase  Idursulfase  [1] D04499 💬  [1] IDS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 315  Jr-171  -  -  -  -  [1] 19 💬 
 316  Kanuma  -  -  -  -  [1] 19 💬 
 317  Lamazym  Velmanase alfa  [1] D11024 💬  [1] MAN2B1 💬  [2] Lysosome, Other glycan degradation  [1] 19 💬 
 318  Laronidase  Laronidase  [1] D04670 💬  [1] IDUA 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [2] 19, 256 💬 
 319  Laronidase ert  Laronidase  [1] D04670 💬  [1] IDUA 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 320  Ledipasvir  Ledipasvir  [1] D10442 💬  -  -  [1] 19 💬 
 321  Ledipasvir/sofosbuvir  Ledipasvir  [2] D10366, D10442 💬  -  -  [1] 19 💬 
 322  Lenograstim  Lenograstim  [1] D03247 💬  [1] CSF3R 💬  [5] Cytokine-cytokine receptor interaction, Hematopoietic cell lineage, JAK-STAT signaling pathway, PI3K-Akt signaling pathway, Pathways in cancer  [7]  2 , 13, 16, 18, 19, 57, 65 💬 
 323  Lentivirus alpha-gal a transduced stem cells  -  -  -  -  [1] 19 💬 
 324  Lentivirus-mediated delivery of arsa to the cns.  -  -  -  -  [1] 19 💬 
 325  Leucine  Leucine  [1] D00030 💬  -  -  [10]  5 ,  6 ,  7 , 19, 96, 97, 127, 283, 284, 299 💬 
 326  Leucovorin  Leucovorin  [3] D01211, D07986, D07987 💬  -  -  [2] 19, 46 💬 
 327  Lipasa ácida lisosómica, esterasa, colesterol (gen humano lipa), lipasa ácida lisosómica (gen humano lipa)  -  -  -  -  [1] 19 💬 
 328  Lisinopril  Lisinopril  [2] D00362, D08131 💬  [1] ACE 💬  [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system  [7] 19, 46, 49, 66, 67, 113, 222 💬 
 329  Lithium carbonate  Carbonate ion  [1] D00801 💬  -  -  [6]  2 , 13, 17, 18, 19, 127 💬 
 330  Lopace  -  -  -  -  [1] 19 💬 
 331  Losartan  Losartan  [2] D00357, D08146 💬  [1] AGTR1 💬  [16] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway  [18] 17, 19, 36, 46, 58, 66, 67, 85, 96, 97, 98, 113, 164, 167, 179, 215, 222, 299 💬 
 332  Losartan and other angiotensin receptor blockers  Angiotensin II  [4] D00150, D00357, D02014, D08146 💬  [2] AGTR1, AGTR2 💬  [16] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway  [1] 19 💬 
 333  Lucerastat  Lucerastat  [1] D11439 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 334  Lys  -  -  -  -  [1] 19 💬 
 335  Lys-saf302  -  -  -  -  [1] 19 💬 
 336  Lysodase  -  -  -  -  [1] 19 💬 
 337  Lysosomal acid lipase, esterase cholesterol (human gene lipa), lysosomal acid lipase (human gene lipa)  Cholesterol  [1] D00040 💬  -  -  [1] 19 💬 
 338  Lysosomal acid lipase, esterase, cholesterol (human gene lipa), lysosomal acid lipase (human gene lipa)  Cholesterol  [1] D00040 💬  -  -  [1] 19 💬 
 339  Mabthera  -  -  -  -  [22] 11, 13, 14, 19, 35, 43, 44, 46, 49, 50, 51, 52, 53, 61, 63, 64, 65, 83, 93, 162, 222, 271 💬 
 340  Mabthera - 2 fiale 100 mg 10 ml  -  -  -  -  [2] 19, 65 💬 
 341  Medication to suppress the immune system  -  -  -  -  [1] 19 💬 
 342  Melphalan  Melphalan  [1] D00369 💬  -  -  [15] 11, 13, 14, 19, 20, 28, 60, 62, 65, 96, 164, 234, 284, 285, 299 💬 
 343  Mepsevii  -  -  -  -  [1] 19 💬 
 344  Mercaptamina  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 345  Mercaptamine  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 346  Mercaptamine bitartrate  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 347  Mercaptamine hydrochloride  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 348  Mercaptamine, mercamine, 2-aminoethanethiol  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 349  Metazym  -  -  -  -  [1] 19 💬 
 350  Methotrexate  Methotrexate  [2] D00142, D02115 💬  [2] DHFR, DHFR2 💬  [5] Antifolate resistance, Biosynthesis of cofactors, Folate biosynthesis, Metabolic pathways, One carbon pool by folate  [35] 11, 13, 19, 34, 35, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 53, 55, 56, 60, 62, 65, 84, 93, 96, 97, 107, 162, 164, 172, 256, 271, 284, 285, 326, 331 💬 
 351  Methylprednisolone  Methylprednisolone  [6] D00407, D00751, D00979, D05000, D05001, D05002 💬  [1] NR3C1 💬  [1] Neuroactive ligand-receptor interaction  [44]  2 ,  6 , 11, 13, 14, 18, 19, 25, 26, 35, 38, 39, 40, 41, 42, 43, 45, 46, 49, 50, 51, 60, 63, 64, 65, 66, 83, 84, 86, 96, 97, 127, 145, 162, 164, 211, 220, 222, 224, 271, 283, 284, 285, 296 💬 
 352  Migalastat  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 353  Migalastat hcl  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 354  Migalastat hcl 150 mg  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 355  Migalastat hydrochloride  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 356  Migalastat hydrocloride  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 357  Miglustat  Miglustat  [1] D05032 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [3] 19, 256, 299 💬 
 358  Miglustat (zavesca)  Miglustat  [1] D05032 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 359  Monitor  Methamidophos  -  -  -  [18]  2 , 11, 13, 19, 46, 49, 58, 65, 70, 85, 86, 98, 113, 118, 129, 298, 299, 300 💬 
 360  Moss-agal (recombinant human alpha-galactosidase a produced in moss)  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 361  Mozobil  -  -  -  -  [3] 19, 65, 285 💬 
 362  Mozobil - 20 mg/ml - soluzione iniettabile - uso sottocutaneo - f  -  -  -  -  [1] 19 💬 
 363  Mycophenolate  Mycophenolic acid  [1] D05096 💬  [2] IMPDH1, IMPDH2 💬  [3] Drug metabolism - other enzymes, Metabolic pathways, Purine metabolism  [34]  2 , 11, 13, 19, 20, 28, 35, 36, 42, 43, 45, 49, 51, 53, 60, 62, 65, 66, 84, 85, 93, 95, 96, 162, 164, 222, 224, 226, 228, 234, 283, 284, 285, 300 💬 
 364  Mycophenolate mofetil  Mycophenolate mofetil  [4] D00752, D05094, D05095, D05096 💬  [2] IMPDH1, IMPDH2 💬  [3] Drug metabolism - other enzymes, Metabolic pathways, Purine metabolism  [32]  2 , 11, 13, 19, 20, 28, 35, 36, 42, 43, 45, 49, 51, 53, 60, 62, 65, 66, 85, 93, 95, 96, 162, 164, 222, 224, 226, 234, 283, 284, 285, 300 💬 
 365  Mycophenylate mofetil  -  -  -  -  [2] 19, 20 💬 
 366  Myelostim - 34 1 flaconcino liofilizzato 33.6 miu + siringa preriempita solvente 1 ml  -  -  -  -  [2] 19, 65 💬 
 367  N acetyl cysteine  Cysteine  [2] D00026, D02326 💬  -  -  [2]  6 , 19 💬 
 368  N acetyl l leucine  Leucine  [1] D00030 💬  -  -  [1] 19 💬 
 369  N-acetyl cysteine  Cysteine  [2] D00026, D02326 💬  -  -  [7] 13, 19, 34, 85, 88, 296, 310 💬 
 370  N-acetyl-l-leucine  Leucine  [1] D00030 💬  -  -  [1] 19 💬 
 371  N-acetylcysteine  Acetylcysteine  [1] D00221 💬  -  -  [10]  6 , 13, 19, 20, 49, 58, 85, 111, 164, 299 💬 
 372  N-acetylgalactosamine 4-sulfatase  -  -  -  -  [1] 19 💬 
 373  N-acetylgalactosamine-6-sulfatase  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 374  Naglazyme  -  -  -  -  [1] 19 💬 
 375  Naglazyme (galsulfase)  Galsulfase  [1] D06565 💬  [1] ARSB 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 376  Naglazyme®  -  -  -  -  [1] 19 💬 
 377  Non applicable  -  -  -  -  [2] 10, 19 💬 
 378  Odiparcil  Odiparcil  -  -  -  [1] 19 💬 
 379  Ogt 918  -  -  -  -  [2] 19, 299 💬 
 380  Ogt918  -  -  -  -  [1] 19 💬 
 381  Ogt923  -  -  -  -  [1] 19 💬 
 382  Olenasufligene relduparvovec  Olenasufligene relduparvovec  -  -  -  [1] 19 💬 
 383  Olipudase alfa  Olipudase alfa  [1] D10820 💬  [1] SMPD1 💬  [5] Lysosome, Metabolic pathways, Necroptosis, Sphingolipid metabolism, Sphingolipid signaling pathway  [1] 19 💬 
 384  Olipudase alfa (rhasm)  Olipudase alfa  [1] D10820 💬  [1] SMPD1 💬  [5] Lysosome, Metabolic pathways, Necroptosis, Sphingolipid metabolism, Sphingolipid signaling pathway  [1] 19 💬 
 385  Omnipaque  -  -  -  -  [1] 19 💬 
 386  Oral migalastat hcl  Migalastat  [1] D10359 💬  -  -  [1] 19 💬 
 387  Osteopetrosis haploidentical only preparative regimen  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 388  Osteopetrosis only preparative regimen  -  -  -  -  [5] 19, 20, 125, 234, 326 💬 
 389  Other: brief pain inventory questionnaire  -  -  -  -  [1] 19 💬 
 390  Other: challenge agent: capsaicin  Capsaicin  [1] D00250 💬  [1] TRPV1 💬  [2] Inflammatory mediator regulation of TRP channels, Neuroactive ligand-receptor interaction  [1] 19 💬 
 391  Other: control  -  -  -  -  [8]  6 , 19, 70, 75, 85, 97, 162, 193 💬 
 392  Other: cysteamine bitartrate  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 393  Other: electroencephalogram (eeg) awake andextended overnight  -  -  -  -  [1] 19 💬 
 394  Other: fluorescein angiography  Fluorescein  [2] D01261, D02024 💬  -  -  [1] 19 💬 
 395  Other: general and neurological examination  -  -  -  -  [1] 19 💬 
 396  Other: ketogenic diet  -  -  -  -  [1] 19 💬 
 397  Other: neurology exam  -  -  -  -  [1] 19 💬 
 398  Other: no it treatment  -  -  -  -  [1] 19 💬 
 399  Other: palliative care  -  -  -  -  [5] 19, 65, 120, 160, 326 💬 
 400  Other: potable water  Water  [1] D00001 💬  -  -  [1] 19 💬 
 401  Other: quality of life questionnaire  -  -  -  -  [1] 19 💬 
 402  Other: sham  -  -  -  -  [2] 19, 301 💬 
 403  Other: vital signs  -  -  -  -  [1] 19 💬 
 404  Otl-200 dispersion for infusion  -  -  -  -  [1] 19 💬 
 405  Oxygen  Oxygen  [1] D00003 💬  -  -  [18]  6 , 13, 19, 46, 49, 70, 84, 85, 86, 88, 90, 96, 97, 193, 226, 294, 299, 330 💬 
 406  Paricalcitol  Paricalcitol  [1] D00930 💬  [1] VDR 💬  [4] Endocrine and other factor-regulated calcium reabsorption, Mineral absorption, Parathyroid hormone synthesis, secretion and action, Tuberculosis  [3] 19, 66, 218 💬 
 407  Pegunigalsidase alfa  Pegunigalsidase alfa  [1] D11685 💬  -  -  [1] 19 💬 
 408  Pegunigalsidase alpha  -  -  -  -  [1] 19 💬 
 409  Pending  -  -  -  -  [6] 13, 19, 96, 97, 113, 302 💬 
 410  Pentosan polysulfat sp 54® injection solution  -  -  -  -  [1] 19 💬 
 411  Pentosan polysulfate  Pentosan polysulfate  [1] D05428 💬  -  -  [3] 19, 26, 226 💬 
 412  Pentosan polysulfate sodium  Pentosan polysulfate  [1] D05428 💬  -  -  [1] 19 💬 
 413  Pentosan polysulphate sp54  -  -  -  -  [1] 19 💬 
 414  Pentosan polysulphate sp54®  -  -  -  -  [1] 19 💬 
 415  Perdix  -  -  -  -  [1] 19 💬 
 416  Plant cell expressed recombinant glucocerebrosidase (prgcd)  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 417  Plant cell recombinant glucocerebrosidase  -  -  -  -  [1] 19 💬 
 418  Plx-200  -  -  -  -  [1] 19 💬 
 419  Pr001  -  -  -  -  [1] 19 💬 
 420  Prednisone  Prednisone  [1] D00473 💬  [1] NR3C1 💬  [1] Neuroactive ligand-receptor interaction  [47]  2 ,  6 , 11, 13, 14, 19, 26, 35, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 53, 61, 63, 64, 65, 66, 81, 84, 85, 86, 93, 95, 96, 97, 113, 127, 162, 164, 222, 224, 228, 251, 283, 284, 285, 288, 299, 300, 331 💬 
 421  Prevenar13  -  -  -  -  [2] 19, 265 💬 
 422  Prgcd  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 423  Procedure: 12 lead electrocardiogram  -  -  -  -  [1] 19 💬 
 424  Procedure: 2-hour holter monitor  Methamidophos  -  -  -  [1] 19 💬 
 425  Procedure: allogeneic stem cell transplantation  -  -  -  -  [3] 19, 20, 62 💬 
 426  Procedure: blood draw  -  -  -  -  [5]  6 , 19, 65, 231, 299 💬 
 427  Procedure: brain mri/mrs/fmri  -  -  -  -  [1] 19 💬 
 428  Procedure: contrast sensitivity measurement  -  -  -  -  [1] 19 💬 
 429  Procedure: dexa scan  -  -  -  -  [3] 19, 46, 96 💬 
 430  Procedure: echocardiogram  -  -  -  -  [1] 19 💬 
 431  Procedure: lumbar puncture  -  -  -  -  [5]  6 , 13, 19, 96, 97 💬 
 432  Procedure: magnetic resonance imaging  -  -  -  -  [1] 19 💬 
 433  Procedure: ophthalmology exam  -  -  -  -  [1] 19 💬 
 434  Procedure: oxygen flow at the optic nerve head measurement  Oxygen  [1] D00003 💬  -  -  [1] 19 💬 
 435  Procedure: quantitative chemical shift imaging (qcsi)  -  -  -  -  [1] 19 💬 
 436  Procedure: skeletal survey  -  -  -  -  [1] 19 💬 
 437  Procedure: skin biopsy  -  -  -  -  [2] 19, 84 💬 
 438  Procedure: slit lamp assessment and intra-ocular pressure measurement  -  -  -  -  [1] 19 💬 
 439  Procedure: speech and modified barium swallow study  Barium  -  -  -  [1] 19 💬 
 440  Procedure: stem cell transplant  -  -  -  -  [5] 19, 20, 65, 164, 284 💬 
 441  Procedure: stem cell transplantation  -  -  -  -  [6] 19, 51, 60, 62, 65, 326 💬 
 442  Procedure: surgery to implant human cns stem cells (hucns-sc)  -  -  -  -  [1] 19 💬 
 443  Procedure: total body irradiation  -  -  -  -  [6] 19, 20, 51, 60, 65, 285 💬 
 444  Procedure: urine collection  -  -  -  -  [1] 19 💬 
 445  Procedure: visual field testing  -  -  -  -  [1] 19 💬 
 446  Procedure: whole body protein turnover  -  -  -  -  [4] 19, 46, 96, 299 💬 
 447  Procysbi  -  -  -  -  [1] 19 💬 
 448  Prx-102  -  -  -  -  [1] 19 💬 
 449  Prx-102 (pegunigalsidase alfa)  Pegunigalsidase alfa  [1] D11685 💬  -  -  [1] 19 💬 
 450  Prx-112  -  -  -  -  [1] 19 💬 
 451  Prx102  -  -  -  -  [1] 19 💬 
 452  Ptc124  -  -  -  -  [4] 19, 113, 246, 299 💬 
 453  Pyrimethamine  Pyrimethamine  [1] D00488 💬  -  -  [4]  2 ,  4 , 19, 65 💬 
 454  Raav 2/6 hids donor  -  -  -  -  [1] 19 💬 
 455  Raav2/5-hnaglu  -  -  -  -  [1] 19 💬 
 456  Raav2/6 left zfn vector  -  -  -  -  [1] 19 💬 
 457  Raav2/6 right zfn vector  -  -  -  -  [1] 19 💬 
 458  Raav9.cmv.hnaglu  -  -  -  -  [1] 19 💬 
 459  Radiation: total body irradiation with marrow boosting  -  -  -  -  [2] 19, 234 💬 
 460  Rebisufligene etisparvovec  -  -  -  -  [1] 19 💬 
 461  Recombinant adeno-associated virus 2/6 vector encoding the cdna for human alpha galactosidase a  -  -  -  -  [1] 19 💬 
 462  Recombinant alpha-galactosidase a  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 463  Recombinant human acid sphingomyelinase (rhasm)  -  -  -  -  [1] 19 💬 
 464  Recombinant human alpha-galactosidase  -  -  -  -  [1] 19 💬 
 465  Recombinant human alpha-galactosidase abbreviated as r-h-alpha-gal  -  -  -  -  [1] 19 💬 
 466  Recombinant human alpha-mannosidase  -  -  -  -  [1] 19 💬 
 467  Recombinant human alpha-n-acetylglucosaminidase (rhnaglu)  -  -  -  -  [1] 19 💬 
 468  Recombinant human arylsulfatase a  -  -  -  -  [1] 19 💬 
 469  Recombinant human arylsulfatase a (rhasa)  -  -  -  -  [1] 19 💬 
 470  Recombinant human arylsulfatase a (rhasa,  -  -  -  -  [1] 19 💬 
 471  Recombinant human arysulfatase b, recombinant human n-acetylgalactosamine 4-sulfatase  -  -  -  -  [1] 19 💬 
 472  Recombinant human beta glucuronidase  -  -  -  -  [1] 19 💬 
 473  Recombinant human beta-glucuronidase  Vestronidase alfa  [1] D11004 💬  [1] GUSB 💬  [8] Ascorbate and aldarate metabolism, Biosynthesis of cofactors, Drug metabolism - other enzymes, Glycosaminoglycan degradation, Lysosome, Metabolic pathways, Pentose and glucuronate interconversions, Porphyrin and chlorophyll metabolism  [1] 19 💬 
 474  Recombinant human beta-glucuronidase (rhgus)  Vestronidase alfa  [1] D11004 💬  [1] GUSB 💬  [8] Ascorbate and aldarate metabolism, Biosynthesis of cofactors, Drug metabolism - other enzymes, Glycosaminoglycan degradation, Lysosome, Metabolic pathways, Pentose and glucuronate interconversions, Porphyrin and chlorophyll metabolism  [1] 19 💬 
 475  Recombinant human betaglucuronidase  -  -  -  -  [1] 19 💬 
 476  Recombinant human derived macrophage-targeted beta-glucocerebrosidase  -  -  -  -  [1] 19 💬 
 477  Recombinant human derived macrophage-targeted ß-glucocerebrosidase  -  -  -  -  [1] 19 💬 
 478  Recombinant human glucerebrosidase  -  -  -  -  [1] 19 💬 
 479  Recombinant human glucocerebrosidase  -  -  -  -  [1] 19 💬 
 480  Recombinant human glucocerebrosidase (prgcd)  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 481  Recombinant human heparan n-sulfatase  -  -  -  -  [1] 19 💬 
 482  Recombinant human heparan n-sulfatase (rhhns)  -  -  -  -  [1] 19 💬 
 483  Recombinant human heparan n-sulfatase [rhhns]  -  -  -  -  [1] 19 💬 
 484  Recombinant human heparan nsulfatase (rhhns)  -  -  -  -  [1] 19 💬 
 485  Recombinant human lysosomal acid lipase  -  -  -  -  [1] 19 💬 
 486  Recombinant human lysosomal acid lipase (rhlal)  -  -  -  -  [1] 19 💬 
 487  Recombinant human lysosomal acid lipase (rhlal), esterase, cholesterol (human gene lipa)  Cholesterol  [1] D00040 💬  -  -  [1] 19 💬 
 488  Recombinant human lysosomal acid lipase (rhlal), esterase, cholesterol (human gene lipa), lysosomal acid lipase (human gene lipa)  Cholesterol  [1] D00040 💬  -  -  [1] 19 💬 
 489  Recombinant human lysosomal alpha-mannosidase  -  -  -  -  [1] 19 💬 
 490  Recombinant human n-acetylgalactosamine 4-sulfatase  -  -  -  -  [1] 19 💬 
 491  Recombinant human n-acetylgalactosamine 6-sulfatase, bmn 110  -  -  -  -  [1] 19 💬 
 492  Recombinant human n-acetylgalactosamine 6-sulfatase, bmn 110 drug substance  -  -  -  -  [1] 19 💬 
 493  Recombinant human n-acetylgalactosamine-6-sulfatase (rhgalns)  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 494  Recombinant human n-acetylgalactosamine-6-sulfatase, bmn 110  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 495  Recombinant human n-acetylgalactosamine-6-sulfatase, bmn 110 drug substance  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 496  Recombinant human nacetylgalactosamine-  -  -  -  -  [1] 19 💬 
 497  Recombinant human tripeptidyl peptidase-1  -  -  -  -  [1] 19 💬 
 498  Recombinant human tripeptidyl peptidase-1 (rhtpp1)  -  -  -  -  [1] 19 💬 
 499  Reduced intensity conditioning  -  -  -  -  [2] 19, 65 💬 
 500  Reminder capsules  -  -  -  -  [1] 19 💬 
 501  Reminder product  -  -  -  -  [1] 19 💬 
 502  Replagal  -  -  -  -  [1] 19 💬 
 503  Replagal (agalsidase alfa)  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 504  Replagal agalsidase alfa  Agalsidase alfa  [1] D02784 💬  [1] GLA 💬  [6] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 505  Rh growth hormone  Somatotropin  [1] D02691 💬  [1] GHR 💬  [5] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway  [1] 19 💬 
 506  Rharsa  -  -  -  -  [1] 19 💬 
 507  Rhasa  -  -  -  -  [1] 19 💬 
 508  Rhasm  -  -  -  -  [1] 19 💬 
 509  Rhgus  -  -  -  -  [1] 19 💬 
 510  Rhhns-10 mg  -  -  -  -  [1] 19 💬 
 511  Rhhns-45 mg  -  -  -  -  [1] 19 💬 
 512  Rhhns-90 mg  -  -  -  -  [1] 19 💬 
 513  Rhidu (recombinant human-alpha-l-iduronidase)  -  -  -  -  [1] 19 💬 
 514  Rhlaman  Velmanase alfa  [1] D11024 💬  [1] MAN2B1 💬  [2] Lysosome, Other glycan degradation  [1] 19 💬 
 515  Rhnaglu  -  -  -  -  [1] 19 💬 
 516  Rhnaglu radiolabelled  -  -  -  -  [1] 19 💬 
 517  Rhnaglu-igf2  -  -  -  -  [1] 19 💬 
 518  Rimiducid  Rimiducid  [1] D11195 💬  [1] CASP9 💬  [34] Alzheimer disease, Amyotrophic lateral sclerosis, Apoptosis, Apoptosis - multiple species, Colorectal cancer, Endometrial cancer, Epstein-Barr virus infection, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Huntington disease, Influenza A, Kaposi sarcoma-associated herpesvirus infection, Legionellosis, Measles, Non-small cell lung cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Parkinson disease, Pathogenic Escherichia coli infection, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Platinum drug resistance, Prion disease, Prostate cancer, Small cell lung cancer, Thyroid hormone signaling pathway, Toxoplasmosis, Tuberculosis, VEGF signaling pathway, Viral myocarditis, p53 signaling pathway  [6] 19, 60, 65, 284, 285, 326 💬 
 519  Rituximab  Rituximab  [1] D02994 💬  [1] MS4A1 💬  [1] Hematopoietic cell lineage  [47] 11, 13, 14, 17, 19, 35, 36, 41, 42, 43, 44, 45, 46, 49, 50, 51, 52, 53, 55, 56, 60, 61, 63, 64, 65, 66, 83, 84, 85, 86, 93, 94, 96, 97, 162, 222, 229, 256, 271, 274, 283, 284, 285, 288, 296, 300, 331 💬 
 520  Rivogenlecleucel  -  -  -  -  [6] 19, 60, 65, 284, 285, 326 💬 
 521  Rp 103  -  -  -  -  [2]  8 , 19 💬 
 522  Rp103  -  -  -  -  [2]  8 , 19 💬 
 523  Rvx000222  -  -  -  -  [1] 19 💬 
 524  Saf-301  -  -  -  -  [1] 19 💬 
 525  Saline solution for injection  -  -  -  -  [1] 19 💬 
 526  Sar402671, gz402671 or gz/sar402671  -  -  -  -  [3]  6 , 19, 67 💬 
 527  Sb-318  -  -  -  -  [1] 19 💬 
 528  Sb-47171  -  -  -  -  [1] 19 💬 
 529  Sb-47898  -  -  -  -  [1] 19 💬 
 530  Sb-913  -  -  -  -  [1] 19 💬 
 531  Sb-a6p-hrl donor vector  -  -  -  -  [1] 19 💬 
 532  Sb-fix  -  -  -  -  [1] 19 💬 
 533  Sb-idua  -  -  -  -  [1] 19 💬 
 534  Sbc-102  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 535  Sbc-102, recombinant human lysosomal acid lipase  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 536  Sbc-103  -  -  -  -  [1] 19 💬 
 537  Scaav9.u1a.hsgsh  -  -  -  -  [1] 19 💬 
 538  Scaav9.u1a.sgsh  -  -  -  -  [1] 19 💬 
 539  Sebelipasa alfa  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 540  Sebelipase alfa  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 541  Sebelipase alfa (sbc-102)  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 542  Sebelipase alfa 0.35 mg/kg  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 543  Sebelipase alfa 1 mg/kg  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 544  Sebelipase alfa 3 mg/kg  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 545  Shp611  -  -  -  -  [1] 19 💬 
 546  Sirolimus  Sirolimus  [1] D00753 💬  [1] MTOR 💬  [50] AMPK signaling pathway, Acute myeloid leukemia, Adipocytokine signaling pathway, Alzheimer disease, Amyotrophic lateral sclerosis, Apelin signaling pathway, Autophagy - animal, Autophagy - other, Breast cancer, Cellular senescence, Central carbon metabolism in cancer, Choline metabolism in cancer, Colorectal cancer, Diabetic cardiomyopathy, EGFR tyrosine kinase inhibitor resistance, Endocrine resistance, ErbB signaling pathway, Gastric cancer, Glioma, Growth hormone synthesis, secretion and action, HIF-1 signaling pathway, Hepatocellular carcinoma, Herpes simplex virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, Huntington disease, Insulin resistance, Insulin signaling pathway, JAK-STAT signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Longevity regulating pathway, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, PD-L1 expression and PD-1 checkpoint pathway in cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Phospholipase D signaling pathway, Prostate cancer, Proteoglycans in cancer, Shigellosis, Spinocerebellar ataxia, Th17 cell differentiation, Thermogenesis, Thyroid hormone signaling pathway, Type II diabetes mellitus, mTOR signaling pathway  [35]  6 , 13, 17, 19, 34, 35, 36, 46, 49, 51, 60, 61, 62, 63, 65, 66, 67, 84, 85, 89, 98, 127, 137, 157, 158, 192, 222, 277, 278, 279, 280, 281, 283, 285, 331 💬 
 547  Sobi003  -  -  -  -  [1] 19 💬 
 548  Sofosbuvir  Sofosbuvir  [1] D10366 💬  -  -  [1] 19 💬 
 549  Somatropin  Somatotropin  [1] D02691 💬  [1] GHR 💬  [5] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway  [16]  2 ,  3 , 19, 46, 74, 75, 78, 96, 113, 187, 193, 195, 265, 274, 276, 299 💬 
 550  Somatropin (dna origin)  Somatotropin  [1] D02691 💬  [1] GHR 💬  [5] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway  [1] 19 💬 
 551  Ss-mercaptoethylamine hydrochloride & 2-aminoethanethiol hydrochloride  Cysteamine  [2] D03634, D03635 💬  -  -  [1] 19 💬 
 552  St-920  -  -  -  -  [1] 19 💬 
 553  Stem cell transplantation  -  -  -  -  [10] 13, 19, 20, 46, 65, 90, 125, 164, 234, 326 💬 
 554  Sub195712  -  -  -  -  [1] 19 💬 
 555  Taliglucerase alfa  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 556  Taliglucerase alfa - recombinant human glucocerebrosidase  Taliglucerase alfa  [1] D09675 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 557  Tbd  -  -  -  -  [4] 19, 86, 276, 299 💬 
 558  Thiotepa  Thiotepa  [1] D00583 💬  -  -  [11] 13, 19, 20, 28, 51, 60, 65, 85, 96, 164, 284 💬 
 559  Thiotepa--escalated dose  Thiotepa  [1] D00583 💬  -  -  [4] 19, 20, 65, 284 💬 
 560  Thiotepa--single daily dose  Thiotepa  [1] D00583 💬  -  -  [4] 19, 20, 65, 284 💬 
 561  Thyroxine  Levothyroxine  [2] D01010, D08125 💬  [2] THRA, THRB 💬  [2] Neuroactive ligand-receptor interaction, Thyroid hormone signaling pathway  [1] 19 💬 
 562  Trappsol cyclo  -  -  -  -  [1] 19 💬 
 563  Treosulfan  Treosulfan  [1] D07253 💬  -  -  [3] 13, 19, 65 💬 
 564  Triapin  -  -  -  -  [1] 19 💬 
 565  Triapin& triapin mite  -  -  -  -  [1] 19 💬 
 566  Tropicamide  Tropicamide  [1] D00397 💬  [5] CHRM1, CHRM2, CHRM3, CHRM4, CHRM5 💬  [13] Alzheimer disease, Calcium signaling pathway, Cholinergic synapse, Gastric acid secretion, Insulin secretion, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway, Pancreatic secretion, Pathways of neurodegeneration - multiple diseases, Regulation of actin cytoskeleton, Salivary secretion, Taste transduction, cAMP signaling pathway  [2]  6 , 19 💬 
 567  Unrelated umbilical cord blood transplant  -  -  -  -  [1] 19 💬 
 568  Uplyso  -  -  -  -  [1] 19 💬 
 569  Usan: sebelipasa alfa  Sebelipase alfa  [1] D10377 💬  [1] LIPA 💬  [3] Cholesterol metabolism, Lysosome, Steroid biosynthesis  [1] 19 💬 
 570  Usan: sebelipase alpha  -  -  -  -  [1] 19 💬 
 571  Ux003  -  -  -  -  [1] 19 💬 
 572  Vector viral adenoasociado de serotipo 9 que contiene el gen de la sulfamidasa humana  -  -  -  -  [1] 19 💬 
 573  Velaglucerase alfa  Velaglucerase alfa  [1] D09029 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 574  Velaglucerase alfa (vpriv)  Velaglucerase alfa  [1] D09029 💬  [1] GBA 💬  [4] Lysosome, Metabolic pathways, Other glycan degradation, Sphingolipid metabolism  [1] 19 💬 
 575  Velaglucerasi alfa  -  -  -  -  [1] 19 💬 
 576  Velmanase alfa  Velmanase alfa  [1] D11024 💬  [1] MAN2B1 💬  [2] Lysosome, Other glycan degradation  [1] 19 💬 
 577  Velmanase alfa (e.g. lamazym)  Velmanase alfa  [1] D11024 💬  [1] MAN2B1 💬  [2] Lysosome, Other glycan degradation  [1] 19 💬 
 578  Venglustat  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [3]  6 , 19, 67 💬 
 579  Venglustat (gz/sar402671)  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 580  Venglustat gz402671  Venglustat  [1] D11633 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [2] 19, 67 💬 
 581  Vimizim® (elosulfase alfa)  Elosulfase alfa  [1] D10333 💬  [1] GALNS 💬  [3] Glycosaminoglycan degradation, Lysosome, Metabolic pathways  [1] 19 💬 
 582  Vitamin d  Vitamin D  -  -  -  [21] 13, 19, 41, 43, 44, 46, 49, 50, 68, 93, 95, 96, 97, 98, 179, 222, 228, 235, 274, 298, 299 💬 
 583  Vorinostat  Vorinostat  [1] D06320 💬  [11] HDAC1, HDAC10, HDAC11, HDAC2, HDAC3, HDAC4, HDAC5, HDAC6, HDAC7, HDAC8, HDAC9 💬  [17] Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis  [3] 19, 75, 96 💬 
 584  Vpriv  -  -  -  -  [1] 19 💬 
 585  Vpriv - 400 u - polvere per soluzione per infusione - uso endovenoso - flaconcino(vetro) 1 flaconcino  -  -  -  -  [1] 19 💬 
 586  Vpriv 400 units powder for solution of infusion  -  -  -  -  [1] 19 💬 
 587  Vpriv ®,  -  -  -  -  [1] 19 💬 
 588  Vpriv®  -  -  -  -  [1] 19 💬 
 589  Vts-270  -  -  -  -  [1] 19 💬 
 590  Warfarin  Warfarin  [3] D00564, D01280, D08682 💬  [2] NQO1, VKORC1 💬  [6] Biosynthesis of cofactors, Fluid shear stress and atherosclerosis, Hepatocellular carcinoma, Metabolic pathways, Pathways in cancer, Ubiquinone and other terpenoid-quinone biosynthesis  [11]  6 ,  8 , 13, 19, 46, 49, 66, 85, 88, 96, 97 💬 
 591  Water  Water  [1] D00001 💬  -  -  [22]  2 ,  5 ,  6 , 13, 17, 19, 35, 46, 51, 53, 56, 57, 63, 65, 67, 78, 84, 96, 97, 226, 278, 299 💬 
 592  Zavesca  -  -  -  -  [3] 19, 256, 299 💬 
 593  Zavesca (miglustat)  Miglustat  [1] D05032 💬  [1] UGCG 💬  [2] Metabolic pathways, Sphingolipid metabolism  [1] 19 💬 
 594  Zavesca 84cps 100mg  -  -  -  -  [1] 19 💬 
 595  Zestoretic 10,20  -  -  -  -  [1] 19 💬 
 596  Zestoric  -  -  -  -  [1] 19 💬 
 597  Zestril  -  -  -  -  [3] 19, 67, 222 💬 

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