Melphalan ( DrugBank: Melphalan )


15 diseases
IDDisease name (Link within this page)Number of trials
11Myasthenia gravis1
13Multiple sclerosis/Neuromyelitis optica2
14Chronic inflammatory demyelinating polyneuropathy1
19Lysosomal storage disease2
20Adrenoleukodystrophy1
28Systemic amyloidosis45
60Aplastic anemia10
62Paroxysmal nocturnal hemoglobinuria2
65Primary immunodeficiency5
96Crohn disease1
164Oculocutaneous albinism3
234Peroxisomal disease (except Adrenoleukodystrophy)1
284Diamond-Blackfan anemia2
285Fanconi anemia3
299Cystic fibrosis1

11. Myasthenia gravis


Clinical trials : 332Drugs : 234 - (DrugBank : 81) / Drug target genes : 45 - Drug target pathways : 127 
No.TrialIDDate_
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13. Multiple sclerosis/Neuromyelitis optica


Clinical trials : 3,340Drugs : 2,163 - (DrugBank : 383) / Drug target genes : 241 - Drug target pathways : 238 
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14. Chronic inflammatory demyelinating polyneuropathy


Clinical trials : 175Drugs : 161 - (DrugBank : 41) / Drug target genes : 13 - Drug target pathways : 24 
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19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
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20. Adrenoleukodystrophy


Clinical trials : 61Drugs : 90 - (DrugBank : 31) / Drug target genes : 23 - Drug target pathways : 126 
No.TrialIDDate_
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28. Systemic amyloidosis


Clinical trials : 267Drugs : 241 - (DrugBank : 77) / Drug target genes : 68 - Drug target pathways : 180 
No.TrialIDDate_
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60. Aplastic anemia


Clinical trials : 245Drugs : 318 - (DrugBank : 86) / Drug target genes : 44 - Drug target pathways : 166 
No.TrialIDDate_
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62. Paroxysmal nocturnal hemoglobinuria


Clinical trials : 292Drugs : 151 - (DrugBank : 49) / Drug target genes : 22 - Drug target pathways : 108 
No.TrialIDDate_
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65. Primary immunodeficiency


Clinical trials : 500Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217 
No.TrialIDDate_
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96. Crohn disease


Clinical trials : 2,442Drugs : 1,278 - (DrugBank : 248) / Drug target genes : 142 - Drug target pathways : 209 
No.TrialIDDate_
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164. Oculocutaneous albinism


Clinical trials : 15Drugs : 54 - (DrugBank : 34) / Drug target genes : 35 - Drug target pathways : 141 
No.TrialIDDate_
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234. Peroxisomal disease (except Adrenoleukodystrophy)


Clinical trials : 39Drugs : 35 - (DrugBank : 12) / Drug target genes : 13 - Drug target pathways : 45 
No.TrialIDDate_
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284. Diamond-Blackfan anemia


Clinical trials : 36Drugs : 95 - (DrugBank : 34) / Drug target genes : 23 - Drug target pathways : 126 
No.TrialIDDate_
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285. Fanconi anemia


Clinical trials : 62Drugs : 93 - (DrugBank : 30) / Drug target genes : 30 - Drug target pathways : 144 
No.TrialIDDate_
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299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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