Ataluren ( DrugBank: Ataluren )


6 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease2
113Muscular dystrophy54
140Dorabe syndrome1
246Methylmalonic acidemia5
299Cystic fibrosis43
329Aniridia2

19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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agemax
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PhaseCountries

113. Muscular dystrophy


Clinical trials : 646Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries

140. Dorabe syndrome


Clinical trials : 116Drugs : 65 - (DrugBank : 17) / Drug target genes : 50 - Drug target pathways : 64 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
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agemax
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gender
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size
PhaseCountries

246. Methylmalonic acidemia


Clinical trials : 23Drugs : 31 - (DrugBank : 8) / Drug target genes : 17 - Drug target pathways : 23 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
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gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries

329. Aniridia


Clinical trials : 3Drugs : 2 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries