PHENYLBUTYRATE ( DrugBank: Phenylbutyrate )


12 diseases
IDDisease name (Link within this page)Number of trials
2Amyotrophic lateral sclerosis13
3Spinal muscular atrophy3
6Parkinson disease1
8Huntington disease1
15Inclusion body myositis1
93Primary biliary cholangitis2
94Primary sclerosing cholangitis2
244Maple syrup urine disease1
251Urea cycle disorder4
297Alagille syndrome2
299Cystic fibrosis3
338Progressive familial intrahepatic cholestasis2

2. Amyotrophic lateral sclerosis


Clinical trials : 645Drugs : 589 - (DrugBank : 163) / Drug target genes : 150 - Drug target pathways : 225 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
Inclusion_
agemax
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Target_
size
PhaseCountries

3. Spinal muscular atrophy


Clinical trials : 237Drugs : 123 - (DrugBank : 29) / Drug target genes : 51 - Drug target pathways : 75 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

6. Parkinson disease


Clinical trials : 2,307Drugs : 2,007 - (DrugBank : 349) / Drug target genes : 188 - Drug target pathways : 199 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
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gender
Target_
size
PhaseCountries

8. Huntington disease


Clinical trials : 242Drugs : 205 - (DrugBank : 62) / Drug target genes : 85 - Drug target pathways : 159 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

15. Inclusion body myositis


Clinical trials : 42Drugs : 33 - (DrugBank : 11) / Drug target genes : 12 - Drug target pathways : 123 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

93. Primary biliary cholangitis


Clinical trials : 298Drugs : 252 - (DrugBank : 59) / Drug target genes : 35 - Drug target pathways : 115 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

94. Primary sclerosing cholangitis


Clinical trials : 148Drugs : 118 - (DrugBank : 39) / Drug target genes : 18 - Drug target pathways : 141 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

244. Maple syrup urine disease


Clinical trial : 1Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

251. Urea cycle disorder


Clinical trials : 54Drugs : 61 - (DrugBank : 15) / Drug target genes : 3 - Drug target pathways : 28 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

297. Alagille syndrome


Clinical trials : 45Drugs : 21 - (DrugBank : 10) / Drug target genes : 3 - Drug target pathways : 5 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

338. Progressive familial intrahepatic cholestasis


Clinical trials : 60Drugs : 26 - (DrugBank : 6) / Drug target genes : 2 - Drug target pathways : 2 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries