Triheptanoin ( DrugBank: Triheptanoin )


10 diseases
IDDisease name (Link within this page)Number of trials
2Amyotrophic lateral sclerosis1
8Huntington disease4
65Primary immunodeficiency1
149Hemiconvulsion hemiplegia epilepsy syndrome1
156Rett syndrome2
248Glucose transporter type 1 deficiency24
256Muscle glycogenosis5
257Hepatic glycogenosis3
317Trifunctional protein deficiency1
324Methylglutaconic aciduria1

2. Amyotrophic lateral sclerosis


Clinical trials : 645Drugs : 589 - (DrugBank : 163) / Drug target genes : 150 - Drug target pathways : 225 
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8. Huntington disease


Clinical trials : 242Drugs : 205 - (DrugBank : 62) / Drug target genes : 85 - Drug target pathways : 159 
No.TrialIDDate_
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65. Primary immunodeficiency


Clinical trials : 500Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217 
No.TrialIDDate_
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149. Hemiconvulsion hemiplegia epilepsy syndrome


Clinical trials : 25Drugs : 35 - (DrugBank : 13) / Drug target genes : 16 - Drug target pathways : 22 
No.TrialIDDate_
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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156. Rett syndrome


Clinical trials : 44Drugs : 61 - (DrugBank : 23) / Drug target genes : 57 - Drug target pathways : 83 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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248. Glucose transporter type 1 deficiency


Clinical trials : 29Drugs : 9 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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256. Muscle glycogenosis


Clinical trials : 180Drugs : 133 - (DrugBank : 29) / Drug target genes : 25 - Drug target pathways : 105 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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257. Hepatic glycogenosis


Clinical trials : 14Drugs : 27 - (DrugBank : 7) / Drug target genes : 3 - Drug target pathways : 8 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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317. Trifunctional protein deficiency


Clinical trials : 4Drugs : 9 - (DrugBank : 4) / Drug target gene : 1 - Drug target pathway : 1 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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324. Methylglutaconic aciduria


Clinical trials : 4Drugs : 4 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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agemin
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agemax
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size
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