Drug Description in Trials / DrugBank / KEGG DRUG


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No. DrugBank 薬物名(臨床試験情報から抽出) KEGG DRUG KEGG GENES KEGG PATHWAY 指定難病告示番号
1 Tofersen
(Antisense Oligonucleotide Inhibitor Of The Expression Of Superoxide Dismutase 1 Gene)
1件: Tofersen1件: Tofersen 💬1件: SOD1 💬8件: Amyotrophic lateral sclerosis, Chemical carcinogenesis - reactive oxygen species, Huntington disease, Longevity regulating pathway - multiple species, Parkinson disease, Pathways of neurodegeneration - multiple diseases, Peroxisome, Prion disease 💬1件: 2 💬
2 Zorevunersen
(18-Mer Antisense Oligonucleotide Complementary To SCN1A mRNA)
1件: STK-001---1件: 140 💬