Gold ( DrugBank: Gold )


43 diseases
IDDisease name (Link within this page)Number of trials
2Amyotrophic lateral sclerosis3
5Progressive supranuclear palsy2
6Parkinson disease17
13Multiple sclerosis/Neuromyelitis optica7
17Multiple system atrophy2
34Neurofibromatosis2
35Pemphigus2
46Malignant rheumatoid arthritis6
49Systemic lupus erythematosus2
50Dermatomyositis2
53Sjogren syndrome2
58Hypertrophic cardiomyopathy1
63Idiopathic thrombocytopenic purpura1
65Primary immunodeficiency2
68Ossification of the ligamentum flavum1
76Pituitary gonadotropin secretion hyperthyroidism4
84Sarcoidosis2
86Pulmonary arterial hypertension5
91Budd-Chiari syndrome1
93Primary biliary cholangitis3
95Autoimmune hepatitis1
96Crohn disease4
97Ulcerative colitis2
98Eosinophilic gastrointestinal disease1
113Muscular dystrophy1
137Focal cortical dysplasia1
158Tuberous sclerosis1
162Pemphigoid1
167Marfan syndrome1
171Wilson disease2
193Prader-Willi syndrome1
218Alport syndrome1
222Primary nephrotic syndrome5
224Purpura nephritis1
226Interstitial cystitis with Hunners ulcer1
227Osler disease1
230Alveolar hypoventilation syndrome1
271Ankylosing spondylitis1
291Hirschsprung disease, entire colon type1
296Biliary atresia9
298Hereditary pancreatitis1
310Congenital anomalies syndrome1
318Citrin deficiency1

2. Amyotrophic lateral sclerosis


Clinical trials : 645Drugs : 589 - (DrugBank : 163) / Drug target genes : 150 - Drug target pathways : 225 
No.TrialIDDate_
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5. Progressive supranuclear palsy


Clinical trials : 89Drugs : 107 - (DrugBank : 40) / Drug target genes : 65 - Drug target pathways : 108 
No.TrialIDDate_
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6. Parkinson disease


Clinical trials : 2,307Drugs : 2,007 - (DrugBank : 349) / Drug target genes : 188 - Drug target pathways : 199 
No.TrialIDDate_
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13. Multiple sclerosis/Neuromyelitis optica


Clinical trials : 3,340Drugs : 2,163 - (DrugBank : 383) / Drug target genes : 241 - Drug target pathways : 238 
No.TrialIDDate_
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17. Multiple system atrophy


Clinical trials : 119Drugs : 138 - (DrugBank : 44) / Drug target genes : 59 - Drug target pathways : 111 
No.TrialIDDate_
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34. Neurofibromatosis


Clinical trials : 133Drugs : 186 - (DrugBank : 67) / Drug target genes : 79 - Drug target pathways : 190 
No.TrialIDDate_
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35. Pemphigus


Clinical trials : 99Drugs : 124 - (DrugBank : 36) / Drug target genes : 23 - Drug target pathways : 169 
No.TrialIDDate_
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46. Malignant rheumatoid arthritis


Clinical trials : 4,356Drugs : 2,567 - (DrugBank : 415) / Drug target genes : 192 - Drug target pathways : 228 
No.TrialIDDate_
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49. Systemic lupus erythematosus


Clinical trials : 993Drugs : 702 - (DrugBank : 184) / Drug target genes : 116 - Drug target pathways : 200 
No.TrialIDDate_
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50. Dermatomyositis


Clinical trials : 194Drugs : 244 - (DrugBank : 89) / Drug target genes : 50 - Drug target pathways : 151 
No.TrialIDDate_
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53. Sjogren syndrome


Clinical trials : 305Drugs : 325 - (DrugBank : 104) / Drug target genes : 58 - Drug target pathways : 188 
No.TrialIDDate_
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58. Hypertrophic cardiomyopathy


Clinical trials : 126Drugs : 135 - (DrugBank : 42) / Drug target genes : 46 - Drug target pathways : 162 
No.TrialIDDate_
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63. Idiopathic thrombocytopenic purpura


Clinical trials : 391Drugs : 235 - (DrugBank : 50) / Drug target genes : 49 - Drug target pathways : 139 
No.TrialIDDate_
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65. Primary immunodeficiency


Clinical trials : 500Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217 
No.TrialIDDate_
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68. Ossification of the ligamentum flavum


Clinical trials : 2Drugs : 4 - (DrugBank : 4) / Drug target gene : 1 - Drug target pathways : 3 
No.TrialIDDate_
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76. Pituitary gonadotropin secretion hyperthyroidism


Clinical trials : 29Drugs : 44 - (DrugBank : 14) / Drug target genes : 5 - Drug target pathways : 15 
No.TrialIDDate_
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84. Sarcoidosis


Clinical trials : 149Drugs : 202 - (DrugBank : 78) / Drug target genes : 66 - Drug target pathways : 169 
No.TrialIDDate_
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86. Pulmonary arterial hypertension


Clinical trials : 1,205Drugs : 684 - (DrugBank : 124) / Drug target genes : 100 - Drug target pathways : 193 
No.TrialIDDate_
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91. Budd-Chiari syndrome


Clinical trials : 4Drugs : 5 - (DrugBank : 4) / Drug target genes : 4 - Drug target pathways : 14 
No.TrialIDDate_
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93. Primary biliary cholangitis


Clinical trials : 298Drugs : 252 - (DrugBank : 59) / Drug target genes : 35 - Drug target pathways : 115 
No.TrialIDDate_
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95. Autoimmune hepatitis


Clinical trials : 52Drugs : 68 - (DrugBank : 27) / Drug target genes : 18 - Drug target pathways : 111 
No.TrialIDDate_
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96. Crohn disease


Clinical trials : 2,442Drugs : 1,278 - (DrugBank : 248) / Drug target genes : 142 - Drug target pathways : 209 
No.TrialIDDate_
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97. Ulcerative colitis


Clinical trials : 2,630Drugs : 1,459 - (DrugBank : 265) / Drug target genes : 144 - Drug target pathways : 202 
No.TrialIDDate_
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98. Eosinophilic gastrointestinal disease


Clinical trials : 172Drugs : 149 - (DrugBank : 39) / Drug target genes : 38 - Drug target pathways : 135 
No.TrialIDDate_
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113. Muscular dystrophy


Clinical trials : 646Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170 
No.TrialIDDate_
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137. Focal cortical dysplasia


Clinical trials : 9Drugs : 5 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 51 
No.TrialIDDate_
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158. Tuberous sclerosis


Clinical trials : 112Drugs : 71 - (DrugBank : 19) / Drug target genes : 35 - Drug target pathways : 118 
No.TrialIDDate_
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162. Pemphigoid


Clinical trials : 90Drugs : 122 - (DrugBank : 47) / Drug target genes : 34 - Drug target pathways : 144 
No.TrialIDDate_
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167. Marfan syndrome


Clinical trials : 21Drugs : 40 - (DrugBank : 11) / Drug target genes : 10 - Drug target pathways : 50 
No.TrialIDDate_
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171. Wilson disease


Clinical trials : 79Drugs : 77 - (DrugBank : 17) / Drug target genes : 6 - Drug target pathways : 30 
No.TrialIDDate_
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193. Prader-Willi syndrome


Clinical trials : 113Drugs : 111 - (DrugBank : 26) / Drug target genes : 48 - Drug target pathways : 102 
No.TrialIDDate_
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218. Alport syndrome


Clinical trials : 30Drugs : 36 - (DrugBank : 15) / Drug target genes : 8 - Drug target pathways : 46 
No.TrialIDDate_
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222. Primary nephrotic syndrome


Clinical trials : 310Drugs : 295 - (DrugBank : 117) / Drug target genes : 63 - Drug target pathways : 194 
No.TrialIDDate_
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224. Purpura nephritis


Clinical trials : 16Drugs : 43 - (DrugBank : 21) / Drug target genes : 15 - Drug target pathways : 58 
No.TrialIDDate_
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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226. Interstitial cystitis with Hunners ulcer


Clinical trials : 145Drugs : 156 - (DrugBank : 51) / Drug target genes : 64 - Drug target pathways : 146 
No.TrialIDDate_
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227. Osler disease


Clinical trials : 56Drugs : 72 - (DrugBank : 21) / Drug target genes : 23 - Drug target pathways : 136 
No.TrialIDDate_
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230. Alveolar hypoventilation syndrome


Clinical trials : 6Drugs : 7 - (DrugBank : 4) / Drug target genes : 16 - Drug target pathways : 26 
No.TrialIDDate_
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271. Ankylosing spondylitis


Clinical trials : 574Drugs : 359 - (DrugBank : 68) / Drug target genes : 41 - Drug target pathways : 146 
No.TrialIDDate_
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291. Hirschsprung disease, entire colon type


Clinical trials : 12Drugs : 24 - (DrugBank : 15) / Drug target gene : 0 - Drug target pathway : 0
No.TrialIDDate_
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296. Biliary atresia


Clinical trials : 71Drugs : 70 - (DrugBank : 39) / Drug target genes : 35 - Drug target pathways : 60 
No.TrialIDDate_
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298. Hereditary pancreatitis


Clinical trials : 95Drugs : 148 - (DrugBank : 51) / Drug target genes : 53 - Drug target pathways : 142 
No.TrialIDDate_
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310. Congenital anomalies syndrome


Clinical trials : 11Drugs : 20 - (DrugBank : 10) / Drug target genes : 3 - Drug target pathways : 7 
No.TrialIDDate_
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318. Citrin deficiency


Clinical trials : 2Drugs : 2 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0
No.TrialIDDate_
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